Cost-effectiveness of velmanase alfa vs. bone marrow transplantation or no causal therapy in patients with mild to moderate alpha-mannosidosis
Alpha-mannosidosis is an inherited rare disorder of mannose-containing oligosaccharides metabolism that is currently treated by enzyme replacement therapy (ERT), bone marrow transplantation (BMT), or supportive therapy (ST). However, the relative cost-effectiveness of these treatment options is yet...
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          | Main Authors: | , , , , | 
|---|---|
| Format: | Article | 
| Language: | English | 
| Published: | Taylor & Francis Group
    
        2023-03-01 | 
| Series: | Biotechnology & Biotechnological Equipment | 
| Subjects: | |
| Online Access: | https://www.tandfonline.com/doi/10.1080/13102818.2023.2271574 | 
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