Effect of nusinersen on pulmonary function in children with spinal muscular atrophy in the plateau region: A pilot study
Background: The drug nusinersen is applied to improve motor function in patients with spinal muscle atrophy (SMA). However, research on the effects of this treatment on lung function is lacking. Aim: To investigate the effect of nusinersen on lung function in children with SMA in the Plateau. Method...
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Main Authors: | Jicai Zhu, Xiaofang Chen, Haoke Sang, Minming Ma, Chunhui Tang |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2025-01-01
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Series: | Heliyon |
Subjects: | |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2405844024174191 |
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