Safety through design: Expanding options for spinal muscular atrophy gene therapy

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Bibliographic Details
Main Authors: Ewout J.N. Groen, Renske I. Wadman
Format: Article
Language:English
Published: Elsevier 2025-09-01
Series:Molecular Therapy: Methods & Clinical Development
Online Access:http://www.sciencedirect.com/science/article/pii/S2329050125001457
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