Current landscape of paroxysmal nocturnal hemoglobinuria in the era of complement inhibitors and regulators

Paroxysmal nocturnal hemoglobinuria (PNH) is a rare blood disorder which is caused by mutations in phosphatidylinositol glycan class A leading to hemolysis of red blood cells via complement inhibition. The first treatment for PNH, eculizumab, was FDA approved in 2007. Since then, many new treatment...

Full description

Saved in:
Bibliographic Details
Main Authors: Julia J. Shi, Yusuf M. Ozcan, Carlos I. Ayala Santos, Hetalkumari Patel, Jamile Shammo, Taha Bat
Format: Article
Language:English
Published: SAGE Publishing 2024-12-01
Series:Therapeutic Advances in Hematology
Online Access:https://doi.org/10.1177/20406207241307500
Tags: Add Tag
No Tags, Be the first to tag this record!