Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling

<b>Objectives</b>: Investigating how nanoparticle systems interact in whole blood (WB) is critical to evaluating the effectiveness of malaria therapy. Methods: We decided to establish a pharmacokinetic/pharmacodynamic (PK/PD) model of the quinine population in WB using <i>Plasmodiu...

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Main Authors: Tamara Ramos Maciel, Ana Claudia Funguetto-Ribeiro, Laura Ben Olivo, Flávia Elizabete Guerra Teixeira, Camila de Oliveira Pacheco, Bibiana Verlindo de Araujo, Sandra Elisa Haas
Format: Article
Language:English
Published: MDPI AG 2024-10-01
Series:Pharmaceutics
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Online Access:https://www.mdpi.com/1999-4923/16/11/1369
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author Tamara Ramos Maciel
Ana Claudia Funguetto-Ribeiro
Laura Ben Olivo
Flávia Elizabete Guerra Teixeira
Camila de Oliveira Pacheco
Bibiana Verlindo de Araujo
Sandra Elisa Haas
author_facet Tamara Ramos Maciel
Ana Claudia Funguetto-Ribeiro
Laura Ben Olivo
Flávia Elizabete Guerra Teixeira
Camila de Oliveira Pacheco
Bibiana Verlindo de Araujo
Sandra Elisa Haas
author_sort Tamara Ramos Maciel
collection DOAJ
description <b>Objectives</b>: Investigating how nanoparticle systems interact in whole blood (WB) is critical to evaluating the effectiveness of malaria therapy. Methods: We decided to establish a pharmacokinetic/pharmacodynamic (PK/PD) model of the quinine population in WB using <i>Plasmodium berghei</i>-infected mice, with a subsequent model comparison for nanocapsules coated with polysorbate (NCP80) or prepared with Eudragit<sup>®</sup> RS (NCEUD). The WB quinine population pharmacokinetic model in rats was developed using plasma and partition coefficients for rat erythrocytes. Mouse WB quinine population PK/PD modeling was developed using allometrically scaled literature-free mouse quinine pharmacokinetic data and covariate values to obtain a WB population pharmacokinetic model for quinine and nanocapsules in mice. This allowed for PK/PD modeling of the quinine population with the WB concentration and parasitemia data in mice. All models were built in NONMEN. <b>Results</b>: The WB quinine concentration profiles in rats were characterized using a two-compartment model. Nanoencapsulation reduced clearance and central compartment volume and increased peripherical compartimental volume. A maximum effect model described the PK/PD of the quinine WB population in mice, demonstrating that NCEUD enhances the antimalarial effect. <b>Conclusions</b>: Quinine WB is a good surrogate for describing the response to exposure in malaria. NCEUD outperformed NCP80 and free quinine, suggesting that cationic surfaces improve the potential for treating malaria.
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spelling doaj-art-9f8eb09493d145a2b3a73912f8ad4f0c2024-11-26T18:17:43ZengMDPI AGPharmaceutics1999-49232024-10-011611136910.3390/pharmaceutics16111369Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD ModelingTamara Ramos Maciel0Ana Claudia Funguetto-Ribeiro1Laura Ben Olivo2Flávia Elizabete Guerra Teixeira3Camila de Oliveira Pacheco4Bibiana Verlindo de Araujo5Sandra Elisa Haas6Pharmacology and Pharmacometric Laboratory, LABFAR, Federal University of Pampa (UNIPAMPA), Uruguaiana 97501-970, RS, BrazilPharmacology and Pharmacometric Laboratory, LABFAR, Federal University of Pampa (UNIPAMPA), Uruguaiana 97501-970, RS, BrazilPharmaceutical Sciences Post Graduate Program, College of Pharmacy, Federal University of Rio Grande do Sul, Porto Alegre 91060-100, RS, BrazilPharmacology and Pharmacometric Laboratory, LABFAR, Federal University of Pampa (UNIPAMPA), Uruguaiana 97501-970, RS, BrazilPharmacology and Pharmacometric Laboratory, LABFAR, Federal University of Pampa (UNIPAMPA), Uruguaiana 97501-970, RS, BrazilPharmaceutical Sciences Post Graduate Program, College of Pharmacy, Federal University of Rio Grande do Sul, Porto Alegre 91060-100, RS, BrazilPharmacology and Pharmacometric Laboratory, LABFAR, Federal University of Pampa (UNIPAMPA), Uruguaiana 97501-970, RS, Brazil<b>Objectives</b>: Investigating how nanoparticle systems interact in whole blood (WB) is critical to evaluating the effectiveness of malaria therapy. Methods: We decided to establish a pharmacokinetic/pharmacodynamic (PK/PD) model of the quinine population in WB using <i>Plasmodium berghei</i>-infected mice, with a subsequent model comparison for nanocapsules coated with polysorbate (NCP80) or prepared with Eudragit<sup>®</sup> RS (NCEUD). The WB quinine population pharmacokinetic model in rats was developed using plasma and partition coefficients for rat erythrocytes. Mouse WB quinine population PK/PD modeling was developed using allometrically scaled literature-free mouse quinine pharmacokinetic data and covariate values to obtain a WB population pharmacokinetic model for quinine and nanocapsules in mice. This allowed for PK/PD modeling of the quinine population with the WB concentration and parasitemia data in mice. All models were built in NONMEN. <b>Results</b>: The WB quinine concentration profiles in rats were characterized using a two-compartment model. Nanoencapsulation reduced clearance and central compartment volume and increased peripherical compartimental volume. A maximum effect model described the PK/PD of the quinine WB population in mice, demonstrating that NCEUD enhances the antimalarial effect. <b>Conclusions</b>: Quinine WB is a good surrogate for describing the response to exposure in malaria. NCEUD outperformed NCP80 and free quinine, suggesting that cationic surfaces improve the potential for treating malaria.https://www.mdpi.com/1999-4923/16/11/1369interspecies translationwhole bloodquininenanocapsulesmalariaPK/PD modeling
spellingShingle Tamara Ramos Maciel
Ana Claudia Funguetto-Ribeiro
Laura Ben Olivo
Flávia Elizabete Guerra Teixeira
Camila de Oliveira Pacheco
Bibiana Verlindo de Araujo
Sandra Elisa Haas
Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
Pharmaceutics
interspecies translation
whole blood
quinine
nanocapsules
malaria
PK/PD modeling
title Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
title_full Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
title_fullStr Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
title_full_unstemmed Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
title_short Improved Malaria Therapy with Cationic Nanocapsules Demonstrated in <i>Plasmodium berghei</i>-Infected Rodents Using Whole Blood Surrogate Population PK/PD Modeling
title_sort improved malaria therapy with cationic nanocapsules demonstrated in i plasmodium berghei i infected rodents using whole blood surrogate population pk pd modeling
topic interspecies translation
whole blood
quinine
nanocapsules
malaria
PK/PD modeling
url https://www.mdpi.com/1999-4923/16/11/1369
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