Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms

Abstract Clonal hematopoiesis of indeterminate potential is the primary pathogenic risk factor for myeloid neoplasms, while heteroplasmy (mutations in a subset of cellular mitochondrial DNA) is another marker of clonal expansion associated with hematological malignancies. We explore how these two ma...

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Main Authors: Yun Soo Hong, Sergiu Pasca, Wen Shi, Daniela Puiu, Nicole J. Lake, Monkol Lek, Meng Ru, Megan L. Grove, Anna Prizment, Corinne E. Joshu, Elizabeth A. Platz, Eliseo Guallar, Dan E. Arking, Lukasz P. Gondek
Format: Article
Language:English
Published: Nature Portfolio 2024-11-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-024-54443-3
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author Yun Soo Hong
Sergiu Pasca
Wen Shi
Daniela Puiu
Nicole J. Lake
Monkol Lek
Meng Ru
Megan L. Grove
Anna Prizment
Corinne E. Joshu
Elizabeth A. Platz
Eliseo Guallar
Dan E. Arking
Lukasz P. Gondek
author_facet Yun Soo Hong
Sergiu Pasca
Wen Shi
Daniela Puiu
Nicole J. Lake
Monkol Lek
Meng Ru
Megan L. Grove
Anna Prizment
Corinne E. Joshu
Elizabeth A. Platz
Eliseo Guallar
Dan E. Arking
Lukasz P. Gondek
author_sort Yun Soo Hong
collection DOAJ
description Abstract Clonal hematopoiesis of indeterminate potential is the primary pathogenic risk factor for myeloid neoplasms, while heteroplasmy (mutations in a subset of cellular mitochondrial DNA) is another marker of clonal expansion associated with hematological malignancies. We explore how these two markers relate and influence myeloid neoplasms incidence, and their role in risk stratification. We find that heteroplasmy is more common in individuals with clonal hematopoiesis of indeterminate potential, particularly those with higher variant allele fractions, multiple mutations, or spliceosome machinery mutations. Individuals with both markers have a higher risk of myeloid neoplasms than those with either alone. Furthermore, heteroplasmic variants with higher predicted deleteriousness increase the risk of myeloid neoplasms. Incorporating heteroplasmy in an existing risk score model for individuals with clonal hematopoiesis of indeterminate potential significantly improves sensitivity and better identifies high-risk groups. This suggests heteroplasmy as a clonal expansion marker and potentially as a biomarker for myeloid neoplasms development.
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spelling doaj-art-7f8586a4638e405dbde112e6a26b0a052024-11-24T12:33:07ZengNature PortfolioNature Communications2041-17232024-11-0115111510.1038/s41467-024-54443-3Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasmsYun Soo Hong0Sergiu Pasca1Wen Shi2Daniela Puiu3Nicole J. Lake4Monkol Lek5Meng Ru6Megan L. Grove7Anna Prizment8Corinne E. Joshu9Elizabeth A. Platz10Eliseo Guallar11Dan E. Arking12Lukasz P. Gondek13McKusick-Nathans Institute, Department of Genetic Medicine, Johns Hopkins University School of MedicineDivision of Hematological Malignancies, Johns Hopkins University School of MedicineMcKusick-Nathans Institute, Department of Genetic Medicine, Johns Hopkins University School of MedicineDepartment of Biomedical Engineering, Johns Hopkins UniversityDepartment of Genetics, Yale School of MedicineDepartment of Genetics, Yale School of MedicineDepartment of Epidemiology, Johns Hopkins Bloomberg School of Public HealthHuman Genetics Center; Department of Epidemiology, Human Genetics, and Environmental Sciences; School of Public Health, The University of Texas Health Science Center at HoustonDepartment of Laboratory Medicine & Pathology, University of Minnesota Medical SchoolSidney Kimmel Comprehensive Cancer Center, Johns Hopkins University School of MedicineSidney Kimmel Comprehensive Cancer Center, Johns Hopkins University School of MedicineDepartment of Epidemiology, School of Global Public Health, New York UniversityMcKusick-Nathans Institute, Department of Genetic Medicine, Johns Hopkins University School of MedicineDivision of Hematological Malignancies, Johns Hopkins University School of MedicineAbstract Clonal hematopoiesis of indeterminate potential is the primary pathogenic risk factor for myeloid neoplasms, while heteroplasmy (mutations in a subset of cellular mitochondrial DNA) is another marker of clonal expansion associated with hematological malignancies. We explore how these two markers relate and influence myeloid neoplasms incidence, and their role in risk stratification. We find that heteroplasmy is more common in individuals with clonal hematopoiesis of indeterminate potential, particularly those with higher variant allele fractions, multiple mutations, or spliceosome machinery mutations. Individuals with both markers have a higher risk of myeloid neoplasms than those with either alone. Furthermore, heteroplasmic variants with higher predicted deleteriousness increase the risk of myeloid neoplasms. Incorporating heteroplasmy in an existing risk score model for individuals with clonal hematopoiesis of indeterminate potential significantly improves sensitivity and better identifies high-risk groups. This suggests heteroplasmy as a clonal expansion marker and potentially as a biomarker for myeloid neoplasms development.https://doi.org/10.1038/s41467-024-54443-3
spellingShingle Yun Soo Hong
Sergiu Pasca
Wen Shi
Daniela Puiu
Nicole J. Lake
Monkol Lek
Meng Ru
Megan L. Grove
Anna Prizment
Corinne E. Joshu
Elizabeth A. Platz
Eliseo Guallar
Dan E. Arking
Lukasz P. Gondek
Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
Nature Communications
title Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
title_full Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
title_fullStr Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
title_full_unstemmed Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
title_short Mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
title_sort mitochondrial heteroplasmy improves risk prediction for myeloid neoplasms
url https://doi.org/10.1038/s41467-024-54443-3
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