Recombinant SMN protein synergizes with spinal muscular atrophy therapy to counteract pathological motor neuron phenotypes

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Bibliographic Details
Main Authors: Liliana Brambilla, Chiara F. Valori, Giulia Guidotti, Francesca Martorana, Claudia Sulmona, Lisa Benedetta De Martini, Anselmo Canciani, Marco Fumagalli, Francesca Talpo, Gerardo Biella, Elisa Di Pasquale, Claudio Iacobucci, Federico Forneris, Haiyan Zhou, Daniela Rossi
Format: Article
Language:English
Published: BMC 2024-12-01
Series:Translational Neurodegeneration
Online Access:https://doi.org/10.1186/s40035-024-00455-4
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