Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study

Background Progression after high-dose melphalan with autologous stem cell transplantation (ASCT) in multiple myeloma (MM) may be due in part to immune dysfunction. Regulatory T (Treg) cells reconstitute rapidly after ASCT and inhibit immune responses against myeloma cells.Methods We performed a ran...

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Main Authors: Justin Kline, Yuanyuan Zha, Benjamin A Derman, Todd M Zimmerman, Rebecca Malloy, Andrzej Jakubowiak, Michael R Bishop
Format: Article
Language:English
Published: BMJ Publishing Group 2020-05-01
Series:Journal for ImmunoTherapy of Cancer
Online Access:https://jitc.bmj.com/content/8/1/e000286.full
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author Justin Kline
Yuanyuan Zha
Benjamin A Derman
Todd M Zimmerman
Rebecca Malloy
Andrzej Jakubowiak
Michael R Bishop
author_facet Justin Kline
Yuanyuan Zha
Benjamin A Derman
Todd M Zimmerman
Rebecca Malloy
Andrzej Jakubowiak
Michael R Bishop
author_sort Justin Kline
collection DOAJ
description Background Progression after high-dose melphalan with autologous stem cell transplantation (ASCT) in multiple myeloma (MM) may be due in part to immune dysfunction. Regulatory T (Treg) cells reconstitute rapidly after ASCT and inhibit immune responses against myeloma cells.Methods We performed a randomized study to evaluate two methods of Treg depletion in patients with MM undergoing ASCT. No Treg depletion was performed in the control ASCT arm. An anti-CD25 monoclonal antibody (basiliximab 20 mg IV) was administered on day +1 post-ASCT in the in vivo Treg depletion (IVTRD) arm. Tregs were depleted from autologous stem cell (ASC) grafts with anti-CD25 microbeads and the CliniMACS device in the ex vivo Treg depletion (EVTRD) arm.Results Fifteen patients were enrolled, five in each arm. The conditioning regimen was melphalan 200 mg/m2. Primary objectives included assessments of efficiency of IVTRD/EVTRD, kinetics of Treg depletion and recovery following ASCT, and safety. EVTRD removed 90% of CD4+CD25+ cells from ASC grafts. IVTRD and EVTRD led to reductions in Treg frequency between days +7 and +90 post-transplant compared with the control (p=0.007 and p<0.001, respectively).Conclusions IVTRD and EVTRD are feasible and significantly reduce and delay Treg recovery post-ASCT for MM, and serve as a platform for using post-transplant immunotherapies to improve post-ASCT outcomes.Trial registration number NCT01526096.
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spelling doaj-art-2a71796b0469427e954363ddde265cbb2024-11-08T23:10:08ZengBMJ Publishing GroupJournal for ImmunoTherapy of Cancer2051-14262020-05-018110.1136/jitc-2019-000286Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot studyJustin Kline0Yuanyuan Zha1Benjamin A Derman2Todd M Zimmerman3Rebecca Malloy4Andrzej Jakubowiak5Michael R Bishop6Aff22 grid.170205.10000000419367822The University of Chicago 5841 S. Maryland Ave 60637 Chicago IL USAComprehensive Cancer Center, University of Chicago, Chicago, Illinois, USA1 Section of Hematology/Oncology, University of Chicago Medical Center, Chicago, Illinois, USA2 BeiGene, San Mateo, CA, United States1 Section of Hematology/Oncology, University of Chicago Medical Center, Chicago, Illinois, USA1 Section of Hematology/Oncology, University of Chicago Medical Center, Chicago, Illinois, USA11 The David and Etta Jonas Center for Cellular Therapy, Chicago, Illinois, USABackground Progression after high-dose melphalan with autologous stem cell transplantation (ASCT) in multiple myeloma (MM) may be due in part to immune dysfunction. Regulatory T (Treg) cells reconstitute rapidly after ASCT and inhibit immune responses against myeloma cells.Methods We performed a randomized study to evaluate two methods of Treg depletion in patients with MM undergoing ASCT. No Treg depletion was performed in the control ASCT arm. An anti-CD25 monoclonal antibody (basiliximab 20 mg IV) was administered on day +1 post-ASCT in the in vivo Treg depletion (IVTRD) arm. Tregs were depleted from autologous stem cell (ASC) grafts with anti-CD25 microbeads and the CliniMACS device in the ex vivo Treg depletion (EVTRD) arm.Results Fifteen patients were enrolled, five in each arm. The conditioning regimen was melphalan 200 mg/m2. Primary objectives included assessments of efficiency of IVTRD/EVTRD, kinetics of Treg depletion and recovery following ASCT, and safety. EVTRD removed 90% of CD4+CD25+ cells from ASC grafts. IVTRD and EVTRD led to reductions in Treg frequency between days +7 and +90 post-transplant compared with the control (p=0.007 and p<0.001, respectively).Conclusions IVTRD and EVTRD are feasible and significantly reduce and delay Treg recovery post-ASCT for MM, and serve as a platform for using post-transplant immunotherapies to improve post-ASCT outcomes.Trial registration number NCT01526096.https://jitc.bmj.com/content/8/1/e000286.full
spellingShingle Justin Kline
Yuanyuan Zha
Benjamin A Derman
Todd M Zimmerman
Rebecca Malloy
Andrzej Jakubowiak
Michael R Bishop
Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
Journal for ImmunoTherapy of Cancer
title Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
title_full Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
title_fullStr Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
title_full_unstemmed Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
title_short Regulatory T-cell depletion in the setting of autologous stem cell transplantation for multiple myeloma: pilot study
title_sort regulatory t cell depletion in the setting of autologous stem cell transplantation for multiple myeloma pilot study
url https://jitc.bmj.com/content/8/1/e000286.full
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