Health care costs of home care enzyme replacement therapy for patients with lysosomal storage diseases in Germany
Abstract Background Lysosomal storage diseases (LSDs) can be treated with intravenous enzyme replacement therapy (ERT). ERT is being administered either in specialized clinics or in the home care setting. Studies indicate that home-based ERT can be considered safe and positively effects patient repo...
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| Main Authors: | Ria Heinrich, Franziska Claus, Tonio Schoenfelder |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
BMC
2024-12-01
|
| Series: | Orphanet Journal of Rare Diseases |
| Subjects: | |
| Online Access: | https://doi.org/10.1186/s13023-024-03492-4 |
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