New opportunities for accessing promising non-oncological orphan drugs

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Bibliographic Details
Main Authors: Carla E.M. Hollak, Carelle C. Reparon-Schuijt, Kathelijn Verdeyen, Lisa J. Deesker, Jaap W. Groothoff, Josephine M.I. Vos, Atse H. Huisman, Silvia van der Flier, Anke A.M.G. Pisters-van Roy
Format: Article
Language:English
Published: Elsevier 2025-05-01
Series:The Lancet Regional Health. Europe
Online Access:http://www.sciencedirect.com/science/article/pii/S2666776225000675
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