Macrophage Inhibitor Clodronate Enhances Liver Transduction of Lentiviral but Not Adeno-Associated Viral Vectors or mRNA Lipid Nanoparticles in Neonatal and Juvenile Mice

Recently approved adeno-associated viral (AAV) vectors for liver monogenic diseases haemophilia A and B are exemplifying the success of liver-directed viral gene therapy. In parallel, additional gene therapy strategies are rapidly emerging to overcome some inherent AAV limitations, such as the non-p...

Full description

Saved in:
Bibliographic Details
Main Authors: Loukia Touramanidou, Sonam Gurung, Claudiu A. Cozmescu, Dany Perocheau, Dale Moulding, Patrick F. Finn, Andrea Frassetto, Simon N. Waddington, Paul Gissen, Julien Baruteau
Format: Article
Language:English
Published: MDPI AG 2024-11-01
Series:Cells
Subjects:
Online Access:https://www.mdpi.com/2073-4409/13/23/1979
Tags: Add Tag
No Tags, Be the first to tag this record!