Macrophage Inhibitor Clodronate Enhances Liver Transduction of Lentiviral but Not Adeno-Associated Viral Vectors or mRNA Lipid Nanoparticles in Neonatal and Juvenile Mice by Loukia Touramanidou, Sonam Gurung, Claudiu A. Cozmescu, Dany Perocheau, Dale Moulding, Patrick F. Finn, Andrea Frassetto, Simon N. Waddington, Paul Gissen, Julien Baruteau

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CRISPR/Cas9 Edition of the <i>F9</i> Gene in Human Mesenchymal Stem Cells for Hemophilia B Therapy by Irving Jair Lara-Navarro, Luis Felipe Jave-Suárez, Juan Antonio Marchal, Ana Rebeca Jaloma-Cruz

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Effective gene therapy for metachromatic leukodystrophy achieved with minimal lentiviral genomic integrations by Lucas Tricoli, Sunetra Sase, Julia L. Hacker, Vi Pham, Maxwell Chappell, Laura Breda, Stephanie N. Hurwitz, Naoto Tanaka, Carlo Castruccio Castracani, Amaliris Guerra, Zhongqi Hou, Lars Schlotawa, Karthikeyan Radhakrishnan, Matthew Hogenauer, Aoife Roche, John Everett, Frederic Bushman, Peter Kurre, Rebecca Ahrens-Nicklas, Laura A. Adang, Adeline L. Vanderver, Stefano Rivella

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Eradication of Cancer Cells Using Doxifluridine and Mesenchymal Stem Cells Expressing Thymidine Phosphorylase by Xutu Wang, Ian Peng, Ching-An Peng

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Hippocampal Viral-Mediated Urokinase Plasminogen Activator (uPA) Overexpression Mitigates Stress-Induced Anxiety and Depression in Rats by Increasing Brain-Derived Neurotrophic Fac... by Amine Bahi, Jean-Luc Dreyer

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First-in-class transactivator-free, doxycycline-inducible IL-18-engineered CAR-T cells for relapsed/refractory B cell lymphomas by Pedro Justicia-Lirio, María Tristán-Manzano, Noelia Maldonado-Pérez, Carmen Barbero-Jiménez, Marina Cortijo-Gutiérrez, Kristina Pavlovic, Francisco J. Molina-Estevez, Pilar Muñoz, Ana Hinckley-Boned, Juan R. Rodriguez-Madoz, Felipe Prosper, Carmen Griñán-Lison, Saúl A. Navarro-Marchal, Carla Panisello, Julia Muñoz-Ballester, Pedro A. González-Sierra, Concha Herrera, Juan A. Marchal, Francisco Martín

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GENE THERAPY IN THALASSEMIA AND HEMOGLOBINOPATHIES by Laura Breda, Roberto Gambari, Stefano Rivella

Subjects: “…ß-thalassemia, sickle cell anemia, hemoglobinopathies, gene transfer, lentiviral vector, gene correction, splice-switching, stop codon readthrough, hematopoietic stem cells, induced pluripotent stem cells (iPS)…”
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Investigating Ultrafiltration Membranes and Operation Modes for Improved Lentiviral Vector Processing by Jennifer J. Labisch, Maria Evangelopoulou, Tobias Schleuß, Andreas Pickl

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Development and validation of a droplet digital PCR method for quantifying lentiviral vector infectious titer by Xueling Wu, Xiaoya Zhou, Yueming Wang, Jian Wu, Qian Liang, Xu Yang, Kehua Zhang, Shufang Meng

Subjects: “…Lentiviral vectors…”
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