Development of a RIPK1 degrader to enhance antitumor immunity

Abstract The scaffolding function of receptor interacting protein kinase 1 (RIPK1) confers intrinsic and extrinsic resistance to immune checkpoint blockades (ICBs) and emerges as a promising target for improving cancer immunotherapies. To address the challenge posed by a poorly defined binding pocke...

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Main Authors: Xin Yu, Dong Lu, Xiaoli Qi, Rishi Ram Paudel, Hanfeng Lin, Bryan L. Holloman, Feng Jin, Longyong Xu, Lang Ding, Weiyi Peng, Meng C. Wang, Xi Chen, Jin Wang
Format: Article
Language:English
Published: Nature Portfolio 2024-12-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-024-55006-2
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author Xin Yu
Dong Lu
Xiaoli Qi
Rishi Ram Paudel
Hanfeng Lin
Bryan L. Holloman
Feng Jin
Longyong Xu
Lang Ding
Weiyi Peng
Meng C. Wang
Xi Chen
Jin Wang
author_facet Xin Yu
Dong Lu
Xiaoli Qi
Rishi Ram Paudel
Hanfeng Lin
Bryan L. Holloman
Feng Jin
Longyong Xu
Lang Ding
Weiyi Peng
Meng C. Wang
Xi Chen
Jin Wang
author_sort Xin Yu
collection DOAJ
description Abstract The scaffolding function of receptor interacting protein kinase 1 (RIPK1) confers intrinsic and extrinsic resistance to immune checkpoint blockades (ICBs) and emerges as a promising target for improving cancer immunotherapies. To address the challenge posed by a poorly defined binding pocket within the intermediate domain of RIPK1, here we harness proteolysis targeting chimera (PROTAC) technology to develop a RIPK1 degrader, LD4172. LD4172 exhibits potent and selective RIPK1 degradation both in vitro and in vivo. Degradation of RIPK1 by LD4172 triggers immunogenic cell death, enhances tumor-infiltrating lymphocyte responses, and sensitizes tumors to anti-PD1 therapy in female C57BL/6J mice. This work reports a RIPK1 degrader that serves as a chemical probe for investigating the scaffolding functions of RIPK1 and as a potential therapeutic agent to enhance tumor responses to ICBs therapy.
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publisher Nature Portfolio
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series Nature Communications
spelling doaj-art-f591d40495ea436785c1c2830080331d2024-12-22T12:35:57ZengNature PortfolioNature Communications2041-17232024-12-0115111410.1038/s41467-024-55006-2Development of a RIPK1 degrader to enhance antitumor immunityXin Yu0Dong Lu1Xiaoli Qi2Rishi Ram Paudel3Hanfeng Lin4Bryan L. Holloman5Feng Jin6Longyong Xu7Lang Ding8Weiyi Peng9Meng C. Wang10Xi Chen11Jin Wang12The Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineDepartment of Molecular and Cellular Biology, Baylor College of MedicineHoward Hughes Medical Institute, Janelia Research CampusDepartment of Biology and Biochemistry, University of HoustonHoward Hughes Medical Institute, Janelia Research CampusDepartment of Molecular and Cellular Biology, Baylor College of MedicineThe Verna and Marrs McLean Department of Biochemistry and Molecular Pharmacology, Baylor College of MedicineAbstract The scaffolding function of receptor interacting protein kinase 1 (RIPK1) confers intrinsic and extrinsic resistance to immune checkpoint blockades (ICBs) and emerges as a promising target for improving cancer immunotherapies. To address the challenge posed by a poorly defined binding pocket within the intermediate domain of RIPK1, here we harness proteolysis targeting chimera (PROTAC) technology to develop a RIPK1 degrader, LD4172. LD4172 exhibits potent and selective RIPK1 degradation both in vitro and in vivo. Degradation of RIPK1 by LD4172 triggers immunogenic cell death, enhances tumor-infiltrating lymphocyte responses, and sensitizes tumors to anti-PD1 therapy in female C57BL/6J mice. This work reports a RIPK1 degrader that serves as a chemical probe for investigating the scaffolding functions of RIPK1 and as a potential therapeutic agent to enhance tumor responses to ICBs therapy.https://doi.org/10.1038/s41467-024-55006-2
spellingShingle Xin Yu
Dong Lu
Xiaoli Qi
Rishi Ram Paudel
Hanfeng Lin
Bryan L. Holloman
Feng Jin
Longyong Xu
Lang Ding
Weiyi Peng
Meng C. Wang
Xi Chen
Jin Wang
Development of a RIPK1 degrader to enhance antitumor immunity
Nature Communications
title Development of a RIPK1 degrader to enhance antitumor immunity
title_full Development of a RIPK1 degrader to enhance antitumor immunity
title_fullStr Development of a RIPK1 degrader to enhance antitumor immunity
title_full_unstemmed Development of a RIPK1 degrader to enhance antitumor immunity
title_short Development of a RIPK1 degrader to enhance antitumor immunity
title_sort development of a ripk1 degrader to enhance antitumor immunity
url https://doi.org/10.1038/s41467-024-55006-2
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