Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation

Abstract Background Non-melanoma skin cancers (NMSC) are the most common malignancies worldwide. While early-stage lesions can be definitively treated with local therapies, advanced stage cutaneous squamous cell carcinoma (cSCC) often requires systemic treatments such as PD-1 inhibitors. These treat...

Full description

Saved in:
Bibliographic Details
Main Authors: Itamar Averbuch, Nofar Edri, Nethanel Asher, Gal Markel, Daniel Hendler, Hadas Ditzian Kugler, Eyal Yosefof, Noga Kurman
Format: Article
Language:English
Published: Springer 2025-07-01
Series:Cancer Immunology, Immunotherapy
Subjects:
Online Access:https://doi.org/10.1007/s00262-025-04115-y
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849332647562575872
author Itamar Averbuch
Nofar Edri
Nethanel Asher
Gal Markel
Daniel Hendler
Hadas Ditzian Kugler
Eyal Yosefof
Noga Kurman
author_facet Itamar Averbuch
Nofar Edri
Nethanel Asher
Gal Markel
Daniel Hendler
Hadas Ditzian Kugler
Eyal Yosefof
Noga Kurman
author_sort Itamar Averbuch
collection DOAJ
description Abstract Background Non-melanoma skin cancers (NMSC) are the most common malignancies worldwide. While early-stage lesions can be definitively treated with local therapies, advanced stage cutaneous squamous cell carcinoma (cSCC) often requires systemic treatments such as PD-1 inhibitors. These treatments may be administered for prolonged durations; this practice may lead to an unnecessary physical and financial toxicity. The purpose of this study was to evaluate the patterns of disease progression after anti-PD-1 therapy discontinuation in this group of patients. Methods This retrospective cohort study included patients diagnosed with advanced cSCC and treated with either cemiplimab or pembrolizumab from 2019 to 2024 at a single university-affiliated tertiary medical center. Results The cohort included 131 patients, with a 73% overall response rate. Among the 86 patients with either partial or complete response as the best response included in the final analysis, 40 (47%) patients had a treatment break for at least 3 months, and 46 (53%) continued without discontinuation to a maximal duration of 2 years. After a median follow-up of 29.9 months, 24 (60%) patients in the break group remained progression-free, systemic treatment-free, and alive throughout the follow-up. Four patients (10%) experienced disease progression. Among these, the best overall response was PR in three patients and CR in one patient. Nine (22.5%) patients died due to non-oncological reasons, two (5%) patients died from an unknown cause, and one (2.5%) due to treatment toxicity. The percentage of patients achieving CR was statistically significantly higher in the break group compared to the no-break group. Conclusions Our findings advocate for a more tailored approach to the duration of PD-1 inhibitor therapy in cSCC, potentially reducing burdens of overtreatment. Future studies regarding establishing robust predictors for safe treatment discontinuation are required to enhance decision-making in clinical practice.
format Article
id doaj-art-f4384a64f5e34e249f12988e1630a080
institution Kabale University
issn 1432-0851
language English
publishDate 2025-07-01
publisher Springer
record_format Article
series Cancer Immunology, Immunotherapy
spelling doaj-art-f4384a64f5e34e249f12988e1630a0802025-08-20T03:46:08ZengSpringerCancer Immunology, Immunotherapy1432-08512025-07-017481710.1007/s00262-025-04115-yClinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalationItamar Averbuch0Nofar Edri1Nethanel Asher2Gal Markel3Daniel Hendler4Hadas Ditzian Kugler5Eyal Yosefof6Noga Kurman7Davidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalDavidoff Cancer Center, Rabin Medical Center – Beilinson HospitalAbstract Background Non-melanoma skin cancers (NMSC) are the most common malignancies worldwide. While early-stage lesions can be definitively treated with local therapies, advanced stage cutaneous squamous cell carcinoma (cSCC) often requires systemic treatments such as PD-1 inhibitors. These treatments may be administered for prolonged durations; this practice may lead to an unnecessary physical and financial toxicity. The purpose of this study was to evaluate the patterns of disease progression after anti-PD-1 therapy discontinuation in this group of patients. Methods This retrospective cohort study included patients diagnosed with advanced cSCC and treated with either cemiplimab or pembrolizumab from 2019 to 2024 at a single university-affiliated tertiary medical center. Results The cohort included 131 patients, with a 73% overall response rate. Among the 86 patients with either partial or complete response as the best response included in the final analysis, 40 (47%) patients had a treatment break for at least 3 months, and 46 (53%) continued without discontinuation to a maximal duration of 2 years. After a median follow-up of 29.9 months, 24 (60%) patients in the break group remained progression-free, systemic treatment-free, and alive throughout the follow-up. Four patients (10%) experienced disease progression. Among these, the best overall response was PR in three patients and CR in one patient. Nine (22.5%) patients died due to non-oncological reasons, two (5%) patients died from an unknown cause, and one (2.5%) due to treatment toxicity. The percentage of patients achieving CR was statistically significantly higher in the break group compared to the no-break group. Conclusions Our findings advocate for a more tailored approach to the duration of PD-1 inhibitor therapy in cSCC, potentially reducing burdens of overtreatment. Future studies regarding establishing robust predictors for safe treatment discontinuation are required to enhance decision-making in clinical practice.https://doi.org/10.1007/s00262-025-04115-yCutaneous squamous cell carcinomaPD-1 inhibitorsAnti-PD-1 therapy discontinuation
spellingShingle Itamar Averbuch
Nofar Edri
Nethanel Asher
Gal Markel
Daniel Hendler
Hadas Ditzian Kugler
Eyal Yosefof
Noga Kurman
Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
Cancer Immunology, Immunotherapy
Cutaneous squamous cell carcinoma
PD-1 inhibitors
Anti-PD-1 therapy discontinuation
title Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
title_full Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
title_fullStr Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
title_full_unstemmed Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
title_short Clinical outcomes following PD-1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma: exploring treatment de-escalation
title_sort clinical outcomes following pd 1 inhibitor elective discontinuation in cutaneous squamous cell carcinoma exploring treatment de escalation
topic Cutaneous squamous cell carcinoma
PD-1 inhibitors
Anti-PD-1 therapy discontinuation
url https://doi.org/10.1007/s00262-025-04115-y
work_keys_str_mv AT itamaraverbuch clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT nofaredri clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT nethanelasher clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT galmarkel clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT danielhendler clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT hadasditziankugler clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT eyalyosefof clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation
AT nogakurman clinicaloutcomesfollowingpd1inhibitorelectivediscontinuationincutaneoussquamouscellcarcinomaexploringtreatmentdeescalation