Paediatric drugs trials in China

Objective Clinical trials of children’s drugs are of great significance to rational drug use in children. However, paediatric drugs trials in China are facing complex challenges. At present, the investigation data on registration status of paediatric drug trials in China are still relatively lacking...

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Main Authors: Wei Zhao, Wei Guo, Guo-Xiang Hao, Xiao-Xiao Yuan, Xi-Yu Quan, Xue-Jie Qi, Tian-You Wang
Format: Article
Language:English
Published: BMJ Publishing Group 2020-02-01
Series:BMJ Paediatrics Open
Online Access:https://bmjpaedsopen.bmj.com/content/4/1/e000618.full
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author Wei Zhao
Wei Guo
Guo-Xiang Hao
Xiao-Xiao Yuan
Xi-Yu Quan
Xue-Jie Qi
Tian-You Wang
author_facet Wei Zhao
Wei Guo
Guo-Xiang Hao
Xiao-Xiao Yuan
Xi-Yu Quan
Xue-Jie Qi
Tian-You Wang
author_sort Wei Zhao
collection DOAJ
description Objective Clinical trials of children’s drugs are of great significance to rational drug use in children. However, paediatric drugs trials in China are facing complex challenges. At present, the investigation data on registration status of paediatric drug trials in China are still relatively lacking, and relevant research is urgently needed.Methods The advanced retrieval function is used to retrieve clinical trials data in the Clinical Trial.gov and Chinese Clinical Trial Registry databases in 22 April 2019. Fifteen key items were analysed to describe trial characteristics, including: registration number, study start date (year), mode of funding, type of disease, medicine type, research stage, research design, sample size, number of experimental groups, placebo group, blind method, implementation centre, child specific, newborn specific and participant age.Results A total of 1388 clinical trials of paediatric drugs conducted in China were registered. The number of paediatric drug trials grew steadily over time, from less than 20 per year before 2005 to more than 100 per year after 2012. Most clinical trials were postmarketing (n=800, 57.6%), single-centre (n=1045, 75.3%), intervention studies (n=1161, 83.6%) without blinded methods (1169, 84.2%) and funded by non-profit organisations (n=838, 60.4%). The number of clinical trials for antineoplastic agents (n=254, 18.3%), anti-infectives (n=156, 11.2%) and vaccines (n=154, 11.1%) is the largest.Conclusion Paediatric drug trials in China made a significant progress in recent years. Innovative method and trial design optimisation should be encouraged to accelerate paediatric clinical research. Pharmaceutical companies need to be further stimulated to carry out more high-quality paediatric clinical trials with support of paediatric drug legislation.
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spelling doaj-art-ecbcbfc8d9154c5383ef1a162186b8c12024-12-01T01:25:09ZengBMJ Publishing GroupBMJ Paediatrics Open2399-97722020-02-014110.1136/bmjpo-2019-000618Paediatric drugs trials in ChinaWei Zhao0Wei Guo1Guo-Xiang Hao2Xiao-Xiao Yuan3Xi-Yu Quan4Xue-Jie Qi5Tian-You Wang611NMPA Key Laboratory for Clinical Research and Evaluation of Innovative Drug, Qilu Hospital of Shandong University, Shandong University, Jinan, ChinaBeijing Institute of Clinical Medicine, Beijing, China3Department of Clinical Pharmacy, Key Laboratory of Chemical Biology (Ministry of Education), School of Pharmaceutical Sciences, Cheeloo College of Medicine, Shandong University, Jinan, China1 Department of Clinical Pharmacy, School of Pharmaceutical Sciences, Shandong University, Jinan, China1 Department of Clinical Pharmacy, School of Pharmaceutical Sciences, Shandong University, Jinan, China1 Department of Clinical Pharmacy, School of Pharmaceutical Sciences, Shandong University, Jinan, China2 Beijing Key Laboratory of Paediatric Hematology Oncology, National Key Discipline of Paediatrics (Capital Medical University), Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing, ChinaObjective Clinical trials of children’s drugs are of great significance to rational drug use in children. However, paediatric drugs trials in China are facing complex challenges. At present, the investigation data on registration status of paediatric drug trials in China are still relatively lacking, and relevant research is urgently needed.Methods The advanced retrieval function is used to retrieve clinical trials data in the Clinical Trial.gov and Chinese Clinical Trial Registry databases in 22 April 2019. Fifteen key items were analysed to describe trial characteristics, including: registration number, study start date (year), mode of funding, type of disease, medicine type, research stage, research design, sample size, number of experimental groups, placebo group, blind method, implementation centre, child specific, newborn specific and participant age.Results A total of 1388 clinical trials of paediatric drugs conducted in China were registered. The number of paediatric drug trials grew steadily over time, from less than 20 per year before 2005 to more than 100 per year after 2012. Most clinical trials were postmarketing (n=800, 57.6%), single-centre (n=1045, 75.3%), intervention studies (n=1161, 83.6%) without blinded methods (1169, 84.2%) and funded by non-profit organisations (n=838, 60.4%). The number of clinical trials for antineoplastic agents (n=254, 18.3%), anti-infectives (n=156, 11.2%) and vaccines (n=154, 11.1%) is the largest.Conclusion Paediatric drug trials in China made a significant progress in recent years. Innovative method and trial design optimisation should be encouraged to accelerate paediatric clinical research. Pharmaceutical companies need to be further stimulated to carry out more high-quality paediatric clinical trials with support of paediatric drug legislation.https://bmjpaedsopen.bmj.com/content/4/1/e000618.full
spellingShingle Wei Zhao
Wei Guo
Guo-Xiang Hao
Xiao-Xiao Yuan
Xi-Yu Quan
Xue-Jie Qi
Tian-You Wang
Paediatric drugs trials in China
BMJ Paediatrics Open
title Paediatric drugs trials in China
title_full Paediatric drugs trials in China
title_fullStr Paediatric drugs trials in China
title_full_unstemmed Paediatric drugs trials in China
title_short Paediatric drugs trials in China
title_sort paediatric drugs trials in china
url https://bmjpaedsopen.bmj.com/content/4/1/e000618.full
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AT xuejieqi paediatricdrugstrialsinchina
AT tianyouwang paediatricdrugstrialsinchina