Successful pregnancy of an SMA type 3 sitter on Nusinersen therapy - a case report
Abstract Background Due to improved treatment options, more SMA patients reach childbearing age. Currently, limited data on pregnant SMA patients is available, especially in relation to disease-modifying therapies (DMT). This case report helps to elucidate new approaches for future guidelines in the...
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Main Authors: | Miriam Hiebeler, Simone Thiele, Maggie C. Walter |
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Format: | Article |
Language: | English |
Published: |
BMC
2025-01-01
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Series: | BMC Neurology |
Subjects: | |
Online Access: | https://doi.org/10.1186/s12883-024-04005-3 |
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