Consensus guidelines on managing Rett syndrome across the lifespan

Background Rett syndrome (RTT) is a severe neurodevelopmental disorder with complex medical comorbidities extending beyond the nervous system requiring the attention of health professionals. There is no peer-reviewed, consensus-based therapeutic guidance to care in RTT. The objective was to provide...

Full description

Saved in:
Bibliographic Details
Main Authors: Mary Jones, Cary Fu, Dallas Armstrong, Eric Marsh, David Lieberman, Kathleen Motil, Rochelle Witt, Shannon Standridge, Paige Nues, Jane Lane, Tristen Dinkel, Monica Coenraads, Jana von Hehn, Katie Hale, Bernhard Suter, Daniel Glaze, Jeffrey Neul, Alan Percy, Timothy Benke
Format: Article
Language:English
Published: BMJ Publishing Group 2020-02-01
Series:BMJ Paediatrics Open
Online Access:https://bmjpaedsopen.bmj.com/content/4/1/e000717.full
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1846148564517912576
author Mary Jones
Cary Fu
Dallas Armstrong
Eric Marsh
David Lieberman
Kathleen Motil
Rochelle Witt
Shannon Standridge
Paige Nues
Jane Lane
Tristen Dinkel
Monica Coenraads
Jana von Hehn
Katie Hale
Bernhard Suter
Daniel Glaze
Jeffrey Neul
Alan Percy
Timothy Benke
author_facet Mary Jones
Cary Fu
Dallas Armstrong
Eric Marsh
David Lieberman
Kathleen Motil
Rochelle Witt
Shannon Standridge
Paige Nues
Jane Lane
Tristen Dinkel
Monica Coenraads
Jana von Hehn
Katie Hale
Bernhard Suter
Daniel Glaze
Jeffrey Neul
Alan Percy
Timothy Benke
author_sort Mary Jones
collection DOAJ
description Background Rett syndrome (RTT) is a severe neurodevelopmental disorder with complex medical comorbidities extending beyond the nervous system requiring the attention of health professionals. There is no peer-reviewed, consensus-based therapeutic guidance to care in RTT. The objective was to provide consensus on guidance of best practice for addressing these concerns.Methods Informed by the literature and using a modified Delphi approach, a consensus process was used to develop guidance for care in RTT by health professionals.Results Typical RTT presents early in childhood in a clinically recognisable fashion. Multisystem comorbidities evolve throughout the lifespan requiring coordination of care between primary care and often multiple subspecialty providers. To assist health professionals and families in seeking best practice, a checklist and detailed references for guidance were developed by consensus.Conclusions The overall multisystem issues of RTT require primary care providers and other health professionals to manage complex medical comorbidities within the context of the whole individual and family. Given the median life expectancy well into the sixth decade, guidance is provided to health professionals to achieve current best possible outcomes for these special-needs individuals.
format Article
id doaj-art-cf674e2501f94e23a3c1e9b1f99a4d48
institution Kabale University
issn 2399-9772
language English
publishDate 2020-02-01
publisher BMJ Publishing Group
record_format Article
series BMJ Paediatrics Open
spelling doaj-art-cf674e2501f94e23a3c1e9b1f99a4d482024-12-01T04:15:07ZengBMJ Publishing GroupBMJ Paediatrics Open2399-97722020-02-014110.1136/bmjpo-2020-000717Consensus guidelines on managing Rett syndrome across the lifespanMary Jones0Cary Fu1Dallas Armstrong2Eric Marsh3David Lieberman4Kathleen Motil5Rochelle Witt6Shannon Standridge7Paige Nues8Jane Lane9Tristen Dinkel10Monica Coenraads11Jana von Hehn12Katie Hale13Bernhard Suter14Daniel Glaze15Jeffrey Neul16Alan Percy17Timothy Benke184 Royal Berkshire Foundation Trust, Reading, UKPediatrics and Neurology, Vanderbilt University Medical Center, Nashville, Tennessee, USANeurology, The Children`s Hospital of Philadelphia, Philadelphia, Pennsylvania, USANeurology, The Children`s Hospital of Philadelphia, Philadelphia, Pennsylvania, USANeurology, Boston Children`s Hospital, Boston, Massachusetts, USAPediatrics, Baylor College of Medicine, Houston, Texas, USANeurology, Boston Children`s Hospital, Boston, Massachusetts, USAPediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, USAInternational Rett Syndrome Foundation, Cincinnati, Ohio, USAUniversity of Alabama at Birmingham, School of Medicine, Civitan International Research Center, Birmingham, Alabama, USANeurology, Children`s Hospital Colorado, Aurora, Colorado, USARett Syndrome Research Trust, New York, New York, USARett Syndrome Research Trust, New York, New York, USAPediatric Medicine, UCSF Benioff Children`s Hospital Oakland, Oakland, California, USAPediatrics and Neurology, Baylor College of Medicine, Houston, Texas, USAPediatrics and Neurology, Baylor College of Medicine, Houston, Texas, USAVanderbilt Kennedy Center, Nashville, Tennessee, USAPediatrics, Neurology, Neurobiology, Genetics, and Psychology, The University of Alabama at Birmingham School of Medicine, Birmingham, Alabama, USANeurology, Children`s Hospital Colorado, Aurora, Colorado, USABackground Rett syndrome (RTT) is a severe neurodevelopmental disorder with complex medical comorbidities extending beyond the nervous system requiring the attention of health professionals. There is no peer-reviewed, consensus-based therapeutic guidance to care in RTT. The objective was to provide consensus on guidance of best practice for addressing these concerns.Methods Informed by the literature and using a modified Delphi approach, a consensus process was used to develop guidance for care in RTT by health professionals.Results Typical RTT presents early in childhood in a clinically recognisable fashion. Multisystem comorbidities evolve throughout the lifespan requiring coordination of care between primary care and often multiple subspecialty providers. To assist health professionals and families in seeking best practice, a checklist and detailed references for guidance were developed by consensus.Conclusions The overall multisystem issues of RTT require primary care providers and other health professionals to manage complex medical comorbidities within the context of the whole individual and family. Given the median life expectancy well into the sixth decade, guidance is provided to health professionals to achieve current best possible outcomes for these special-needs individuals.https://bmjpaedsopen.bmj.com/content/4/1/e000717.full
spellingShingle Mary Jones
Cary Fu
Dallas Armstrong
Eric Marsh
David Lieberman
Kathleen Motil
Rochelle Witt
Shannon Standridge
Paige Nues
Jane Lane
Tristen Dinkel
Monica Coenraads
Jana von Hehn
Katie Hale
Bernhard Suter
Daniel Glaze
Jeffrey Neul
Alan Percy
Timothy Benke
Consensus guidelines on managing Rett syndrome across the lifespan
BMJ Paediatrics Open
title Consensus guidelines on managing Rett syndrome across the lifespan
title_full Consensus guidelines on managing Rett syndrome across the lifespan
title_fullStr Consensus guidelines on managing Rett syndrome across the lifespan
title_full_unstemmed Consensus guidelines on managing Rett syndrome across the lifespan
title_short Consensus guidelines on managing Rett syndrome across the lifespan
title_sort consensus guidelines on managing rett syndrome across the lifespan
url https://bmjpaedsopen.bmj.com/content/4/1/e000717.full
work_keys_str_mv AT maryjones consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT caryfu consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT dallasarmstrong consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT ericmarsh consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT davidlieberman consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT kathleenmotil consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT rochellewitt consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT shannonstandridge consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT paigenues consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT janelane consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT tristendinkel consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT monicacoenraads consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT janavonhehn consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT katiehale consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT bernhardsuter consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT danielglaze consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT jeffreyneul consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT alanpercy consensusguidelinesonmanagingrettsyndromeacrossthelifespan
AT timothybenke consensusguidelinesonmanagingrettsyndromeacrossthelifespan