Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.

<h4>Background</h4>To date, there has been no medication that has prevented the progression of Parkinson's disease (PD). Many benefits of intensive and multidisciplinary rehabilitation program for PD are supported by clinical, epidemiological, and experimental data. The main questio...

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Main Authors: Francesca Lea Saibene, Cristina Agliardi, Anna Salvatore, Pietro Arcuri, Anna Castagna, Silvia Gobbo, Federico Merlo, Thomas Bowman, Denise Anastasi, Chiara Pagliari, Elisabetta Farina, Margherita Alberoni, Elena Calabrese, Francesca La Rosa, Chiara Arienti, Marina Saresella, Franca Rosa Guerini, Davide Cattaneo, Francesca Baglio, Mario Clerici, Jorge Navarro, Mario Meloni
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2024-01-01
Series:PLoS ONE
Online Access:https://doi.org/10.1371/journal.pone.0309405
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author Francesca Lea Saibene
Cristina Agliardi
Anna Salvatore
Pietro Arcuri
Anna Castagna
Silvia Gobbo
Federico Merlo
Thomas Bowman
Denise Anastasi
Chiara Pagliari
Elisabetta Farina
Margherita Alberoni
Elena Calabrese
Francesca La Rosa
Chiara Arienti
Marina Saresella
Franca Rosa Guerini
Davide Cattaneo
Francesca Baglio
Mario Clerici
Jorge Navarro
Mario Meloni
author_facet Francesca Lea Saibene
Cristina Agliardi
Anna Salvatore
Pietro Arcuri
Anna Castagna
Silvia Gobbo
Federico Merlo
Thomas Bowman
Denise Anastasi
Chiara Pagliari
Elisabetta Farina
Margherita Alberoni
Elena Calabrese
Francesca La Rosa
Chiara Arienti
Marina Saresella
Franca Rosa Guerini
Davide Cattaneo
Francesca Baglio
Mario Clerici
Jorge Navarro
Mario Meloni
author_sort Francesca Lea Saibene
collection DOAJ
description <h4>Background</h4>To date, there has been no medication that has prevented the progression of Parkinson's disease (PD). Many benefits of intensive and multidisciplinary rehabilitation program for PD are supported by clinical, epidemiological, and experimental data. The main question is whether high-intensity motor and cognitive exercises have an effect on the disease's biological mechanisms.<h4>Objective</h4>This study protocol is a Randomized Controlled Trial (RCT) designed to determine the efficacy of an experimental, intensive, and multidisciplinary treatment in comparison to a home-based self-treatment in improving biomolecular and functional parameters in PD.<h4>Methods</h4>A total of 72 participants will be randomly allocated to two different groups, experimental (n = 36) and control group (n = 36). The rehabilitation program will last 6 consecutive weeks and will involve the execution of a total of 30 sessions, one for each day of the week from Monday to Friday. Participants allocated to the control group will carry out a home-based self-treatment program that includes muscle-stretching and active mobilization exercises for 40'/day for 6 consecutive weeks. The primary outcome measure is the effects of both treatments on a new set of molecular biomarkers such as oligomeric alpha-synuclein and neurotrophic factors measured in peripheral neural derived extracellular vesicles (NDEVs). Secondary outcomes will include changes of motor and non-motor symptoms, balance and gait performance and cognitive functioning. This RCT has been registered as "Intensive Multidisciplinary Rehabilitation and Biomarkers in Parkinson's Disease" on 30 May, 2022 to ClinicalTrials.gov with the Study ID number: NCT05452655.<h4>Discussion</h4>This rehabilitation program is believed to be crucial in modifying biomolecular and functional parameters in people with PD. We expect that this study will provide additional evidence to understand the impact of an aerobic and intensive rehabilitation program on brain plasticity in patients with PD.
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spelling doaj-art-ca46a6b2077e413cb395b9e874804e7a2024-11-17T05:31:17ZengPublic Library of Science (PLoS)PLoS ONE1932-62032024-01-011910e030940510.1371/journal.pone.0309405Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.Francesca Lea SaibeneCristina AgliardiAnna SalvatorePietro ArcuriAnna CastagnaSilvia GobboFederico MerloThomas BowmanDenise AnastasiChiara PagliariElisabetta FarinaMargherita AlberoniElena CalabreseFrancesca La RosaChiara ArientiMarina SaresellaFranca Rosa GueriniDavide CattaneoFrancesca BaglioMario ClericiJorge NavarroMario Meloni<h4>Background</h4>To date, there has been no medication that has prevented the progression of Parkinson's disease (PD). Many benefits of intensive and multidisciplinary rehabilitation program for PD are supported by clinical, epidemiological, and experimental data. The main question is whether high-intensity motor and cognitive exercises have an effect on the disease's biological mechanisms.<h4>Objective</h4>This study protocol is a Randomized Controlled Trial (RCT) designed to determine the efficacy of an experimental, intensive, and multidisciplinary treatment in comparison to a home-based self-treatment in improving biomolecular and functional parameters in PD.<h4>Methods</h4>A total of 72 participants will be randomly allocated to two different groups, experimental (n = 36) and control group (n = 36). The rehabilitation program will last 6 consecutive weeks and will involve the execution of a total of 30 sessions, one for each day of the week from Monday to Friday. Participants allocated to the control group will carry out a home-based self-treatment program that includes muscle-stretching and active mobilization exercises for 40'/day for 6 consecutive weeks. The primary outcome measure is the effects of both treatments on a new set of molecular biomarkers such as oligomeric alpha-synuclein and neurotrophic factors measured in peripheral neural derived extracellular vesicles (NDEVs). Secondary outcomes will include changes of motor and non-motor symptoms, balance and gait performance and cognitive functioning. This RCT has been registered as "Intensive Multidisciplinary Rehabilitation and Biomarkers in Parkinson's Disease" on 30 May, 2022 to ClinicalTrials.gov with the Study ID number: NCT05452655.<h4>Discussion</h4>This rehabilitation program is believed to be crucial in modifying biomolecular and functional parameters in people with PD. We expect that this study will provide additional evidence to understand the impact of an aerobic and intensive rehabilitation program on brain plasticity in patients with PD.https://doi.org/10.1371/journal.pone.0309405
spellingShingle Francesca Lea Saibene
Cristina Agliardi
Anna Salvatore
Pietro Arcuri
Anna Castagna
Silvia Gobbo
Federico Merlo
Thomas Bowman
Denise Anastasi
Chiara Pagliari
Elisabetta Farina
Margherita Alberoni
Elena Calabrese
Francesca La Rosa
Chiara Arienti
Marina Saresella
Franca Rosa Guerini
Davide Cattaneo
Francesca Baglio
Mario Clerici
Jorge Navarro
Mario Meloni
Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
PLoS ONE
title Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
title_full Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
title_fullStr Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
title_full_unstemmed Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
title_short Investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with Parkinson's disease: Study protocol for a phase III randomized controlled clinical trial.
title_sort investigating the effects of a daily multidisciplinary intensive outpatient rehabilitation program on innovative biomarkers in people with parkinson s disease study protocol for a phase iii randomized controlled clinical trial
url https://doi.org/10.1371/journal.pone.0309405
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