Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study

ABSTRACT Acetylcholinesterase inhibitors (AChEIs) remain the first‐line treatment for Alzheimer's disease. However, these drugs are largely symptomatic and often associated with adverse effects. This study aimed to evaluate novel pharmacophores for their in vitro AChEI activity, blood–brain bar...

Full description

Saved in:
Bibliographic Details
Main Authors: L. M. Maboko, A. Theron, J.‐L. Panayides, W. Cordier, D. Fisher, V. Steenkamp
Format: Article
Language:English
Published: Wiley 2024-12-01
Series:Pharmacology Research & Perspectives
Subjects:
Online Access:https://doi.org/10.1002/prp2.70043
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1846126160709156864
author L. M. Maboko
A. Theron
J.‐L. Panayides
W. Cordier
D. Fisher
V. Steenkamp
author_facet L. M. Maboko
A. Theron
J.‐L. Panayides
W. Cordier
D. Fisher
V. Steenkamp
author_sort L. M. Maboko
collection DOAJ
description ABSTRACT Acetylcholinesterase inhibitors (AChEIs) remain the first‐line treatment for Alzheimer's disease. However, these drugs are largely symptomatic and often associated with adverse effects. This study aimed to evaluate novel pharmacophores for their in vitro AChEI activity, blood–brain barrier (BBB) permeability, and cytotoxic potential, hypothesizing that a combination of AChEIs could enhance symptom management while minimizing toxicity. A library of 1453 synthetic pharmacophores was assessed using in vitro and in silico methods to determine their feasibility as an inhibitor of the AChE enzyme. An in‐house miniaturized Ellman's assay determined acellular AChEI activities, while pharmacokinetic properties were evaluated using the SwissADME web tool. The combinational effects of in silico BBB‐permeable pharmacophores and donepezil were examined using a checkerboard AChEI assay. Cytotoxicity of active compounds and their synergistic combinations was assessed in SH‐SY5Y neuroblastoma and bEnd.5 cells using the sulforhodamine B assay. Cellular AChEI activity of active in silico BBB‐permeable predicted compounds was determined using an SH‐SY5Y AChE‐based assay. An in vitro BBB model was used to assess the effect of compounds on the integrity of the bEnd.5 monolayer. Out of the screened compounds, 12 demonstrated 60% AChEI activity at 5 μM, with compound A51 showing the lowest IC50 (0.20 μM). Five compounds were identified as BBB‐permeable, with the donepezil‐C53 combination at ¼IC50 exhibiting the strongest synergy (CI = 0.82). Compounds A136 and C129, either alone or with donepezil, showed cytotoxicity. Notably, compound C53, both alone and in combination with donepezil, demonstrated high AChEI activity and promising BBB permeability, warranting further investigation.
format Article
id doaj-art-c601a6189c364fd68ffae00f87743cc0
institution Kabale University
issn 2052-1707
language English
publishDate 2024-12-01
publisher Wiley
record_format Article
series Pharmacology Research & Perspectives
spelling doaj-art-c601a6189c364fd68ffae00f87743cc02024-12-13T03:28:40ZengWileyPharmacology Research & Perspectives2052-17072024-12-01126n/an/a10.1002/prp2.70043Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico StudyL. M. Maboko0A. Theron1J.‐L. Panayides2W. Cordier3D. Fisher4V. Steenkamp5Department of Pharmacology, School of Medicine, Faculty of Health Sciences University of Pretoria Pretoria South AfricaFuture Production: Chemicals, Council for Scientific and Industrial Research Pretoria South AfricaFuture Production: Chemicals, Council for Scientific and Industrial Research Pretoria South AfricaDepartment of Pharmacology, School of Medicine, Faculty of Health Sciences University of Pretoria Pretoria South AfricaDepartment of Medical BioSciences, Faculty of Natural Sciences, Neurobiology Research Group University of Western Cape Cape Town South AfricaDepartment of Pharmacology, School of Medicine, Faculty of Health Sciences University of Pretoria Pretoria South AfricaABSTRACT Acetylcholinesterase inhibitors (AChEIs) remain the first‐line treatment for Alzheimer's disease. However, these drugs are largely symptomatic and often associated with adverse effects. This study aimed to evaluate novel pharmacophores for their in vitro AChEI activity, blood–brain barrier (BBB) permeability, and cytotoxic potential, hypothesizing that a combination of AChEIs could enhance symptom management while minimizing toxicity. A library of 1453 synthetic pharmacophores was assessed using in vitro and in silico methods to determine their feasibility as an inhibitor of the AChE enzyme. An in‐house miniaturized Ellman's assay determined acellular AChEI activities, while pharmacokinetic properties were evaluated using the SwissADME web tool. The combinational effects of in silico BBB‐permeable pharmacophores and donepezil were examined using a checkerboard AChEI assay. Cytotoxicity of active compounds and their synergistic combinations was assessed in SH‐SY5Y neuroblastoma and bEnd.5 cells using the sulforhodamine B assay. Cellular AChEI activity of active in silico BBB‐permeable predicted compounds was determined using an SH‐SY5Y AChE‐based assay. An in vitro BBB model was used to assess the effect of compounds on the integrity of the bEnd.5 monolayer. Out of the screened compounds, 12 demonstrated 60% AChEI activity at 5 μM, with compound A51 showing the lowest IC50 (0.20 μM). Five compounds were identified as BBB‐permeable, with the donepezil‐C53 combination at ¼IC50 exhibiting the strongest synergy (CI = 0.82). Compounds A136 and C129, either alone or with donepezil, showed cytotoxicity. Notably, compound C53, both alone and in combination with donepezil, demonstrated high AChEI activity and promising BBB permeability, warranting further investigation.https://doi.org/10.1002/prp2.70043acetylcholinesterase inhibitionblood–brain barriercytotoxicitysynthetic compounds
spellingShingle L. M. Maboko
A. Theron
J.‐L. Panayides
W. Cordier
D. Fisher
V. Steenkamp
Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
Pharmacology Research & Perspectives
acetylcholinesterase inhibition
blood–brain barrier
cytotoxicity
synthetic compounds
title Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
title_full Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
title_fullStr Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
title_full_unstemmed Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
title_short Evaluating Blood–Brain Barrier Permeability, Cytotoxicity, and Activity of Potential Acetylcholinesterase Inhibitors: In Vitro and In Silico Study
title_sort evaluating blood brain barrier permeability cytotoxicity and activity of potential acetylcholinesterase inhibitors in vitro and in silico study
topic acetylcholinesterase inhibition
blood–brain barrier
cytotoxicity
synthetic compounds
url https://doi.org/10.1002/prp2.70043
work_keys_str_mv AT lmmaboko evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy
AT atheron evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy
AT jlpanayides evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy
AT wcordier evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy
AT dfisher evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy
AT vsteenkamp evaluatingbloodbrainbarrierpermeabilitycytotoxicityandactivityofpotentialacetylcholinesteraseinhibitorsinvitroandinsilicostudy