Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis

<p><strong>Objective:</strong> Dimethyl fumarate is a medication approved for the treatment of relapsing-remitting multiple sclerosis. The purpose of the study was to evaluate the safety and persistence of dimethyl fumarate in clinical practice and analyze the occurrence of ly...

Full description

Saved in:
Bibliographic Details
Main Authors: Silvia Boullosa-Lale, Lara González-Freire, Luciano Martínez-Martínez, Carlos Crespo-Diz
Format: Article
Language:English
Published: Elsevier 2021-03-01
Series:Farmacia Hospitalaria
Subjects:
Online Access:http://www.aulamedica.es/fh/pdf/11567.pdf
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1846093793682522112
author Silvia Boullosa-Lale
Lara González-Freire
Luciano Martínez-Martínez
Carlos Crespo-Diz
author_facet Silvia Boullosa-Lale
Lara González-Freire
Luciano Martínez-Martínez
Carlos Crespo-Diz
author_sort Silvia Boullosa-Lale
collection DOAJ
description <p><strong>Objective:</strong> Dimethyl fumarate is a medication approved for the treatment of relapsing-remitting multiple sclerosis. The purpose of the study was to evaluate the safety and persistence of dimethyl fumarate in clinical practice and analyze the occurrence of lymphopenia is patients treated with dimethyl fumarate over a period of at least 6 months.</p><p><strong>Method:</strong> This is a retrospective longitudinal observational study carried out between August 2015 and March 2019. The study cohort was made up of patients who had been treated with dimethyl fumarate for at least 6 months. Lymphocyte counts were recorded at different points of time (pre-treatment, at 3, 6, 12 months, and at the end of the study period). The evolution of lymphopenia was evaluated by means of a logistic regression statistical model. An analysis was performed of the relationship between a decreased lymphocyte count over the first 6 months of treatment and the development, by the end of the study, of grade II-III lymphopenia necessitating discontinuation of dimethyl fumarate. Other safety indicators were also evaluated including adverse events and interruptions or discontinuations of treatment. Persistence was determined by measuring the time to discontinuation of treatment.</p><p><strong>Results:</strong> The study included a total of 55 patients, of whom 80% were female. The most common adverse events were lymphopenia (27), rubefaction (16), digestive symptoms (11), fatigue (9), headache (3) and sleep disturbances (2). Eleven subjects interrupted/discontinued their treatment during the study period; reasons were as follows: pregnancy (2), personal decision (2), John Cunningham virus infection (1), allergy to the drug (2), and lymphopenia (4). Median duration of treatment was 23 months (4-43 months). A statistically significant association was found between a lower lymphocyte count over the first 6 months of treatment and the development of severe lymphopenia by the end of the study [OR = 1.34 (0.35-2.60); 95% CI (p = 0.001)].</p><p><strong>Conclusions:</strong> The adverse events observed in the present study are in line with those reported in previous analyses. Lymphopenia was the most common adverse event. The persistence of the medication was similar to that found in pivotal trials. The significant association found between a decreased lymphocyte count over the first 6 months of treatment and the development of severe lymphopenia by the end of the study suggests a connection between both variables, which could be instrumental in being able to predict and even prevent the occurrence of such lymphopenias.</p><p> </p>
format Article
id doaj-art-9e0e047fa75d4d858d636b1d93616f26
institution Kabale University
issn 1130-6343
2171-8695
language English
publishDate 2021-03-01
publisher Elsevier
record_format Article
series Farmacia Hospitalaria
spelling doaj-art-9e0e047fa75d4d858d636b1d93616f262025-01-02T16:24:36ZengElsevierFarmacia Hospitalaria1130-63432171-86952021-03-01452737610.7399/fh.11567Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosisSilvia Boullosa-Lale0Lara González-Freire1Luciano Martínez-Martínez2Carlos Crespo-Diz3Complejo Hospitalario Universitario de Pontevedra, Pontevedra. Spain.Complejo Hospitalario Universitario de Pontevedra, Pontevedra. Spain. Instituto de Investigación Sanitaria Galicia Sur, Fundación Biomédica Galicia Sur, Vigo. Spain.Complejo Hospitalario Universitario de Pontevedra, Pontevedra. Spain.Complejo Hospitalario Universitario de Pontevedra, Pontevedra. Spain. Instituto de Investigación Sanitaria Galicia Sur, Fundación Biomédica Galicia Sur, Vigo. Spain.<p><strong>Objective:</strong> Dimethyl fumarate is a medication approved for the treatment of relapsing-remitting multiple sclerosis. The purpose of the study was to evaluate the safety and persistence of dimethyl fumarate in clinical practice and analyze the occurrence of lymphopenia is patients treated with dimethyl fumarate over a period of at least 6 months.</p><p><strong>Method:</strong> This is a retrospective longitudinal observational study carried out between August 2015 and March 2019. The study cohort was made up of patients who had been treated with dimethyl fumarate for at least 6 months. Lymphocyte counts were recorded at different points of time (pre-treatment, at 3, 6, 12 months, and at the end of the study period). The evolution of lymphopenia was evaluated by means of a logistic regression statistical model. An analysis was performed of the relationship between a decreased lymphocyte count over the first 6 months of treatment and the development, by the end of the study, of grade II-III lymphopenia necessitating discontinuation of dimethyl fumarate. Other safety indicators were also evaluated including adverse events and interruptions or discontinuations of treatment. Persistence was determined by measuring the time to discontinuation of treatment.</p><p><strong>Results:</strong> The study included a total of 55 patients, of whom 80% were female. The most common adverse events were lymphopenia (27), rubefaction (16), digestive symptoms (11), fatigue (9), headache (3) and sleep disturbances (2). Eleven subjects interrupted/discontinued their treatment during the study period; reasons were as follows: pregnancy (2), personal decision (2), John Cunningham virus infection (1), allergy to the drug (2), and lymphopenia (4). Median duration of treatment was 23 months (4-43 months). A statistically significant association was found between a lower lymphocyte count over the first 6 months of treatment and the development of severe lymphopenia by the end of the study [OR = 1.34 (0.35-2.60); 95% CI (p = 0.001)].</p><p><strong>Conclusions:</strong> The adverse events observed in the present study are in line with those reported in previous analyses. Lymphopenia was the most common adverse event. The persistence of the medication was similar to that found in pivotal trials. The significant association found between a decreased lymphocyte count over the first 6 months of treatment and the development of severe lymphopenia by the end of the study suggests a connection between both variables, which could be instrumental in being able to predict and even prevent the occurrence of such lymphopenias.</p><p> </p>http://www.aulamedica.es/fh/pdf/11567.pdfdimethyl fumaraterelapsing remitting multiple sclerosisdrug safetylymphopeniaadverse drug eventstoxicity
spellingShingle Silvia Boullosa-Lale
Lara González-Freire
Luciano Martínez-Martínez
Carlos Crespo-Diz
Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
Farmacia Hospitalaria
dimethyl fumarate
relapsing remitting multiple sclerosis
drug safety
lymphopenia
adverse drug events
toxicity
title Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
title_full Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
title_fullStr Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
title_full_unstemmed Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
title_short Safety and persistence of dimethyl fumarate as a treatment for relapsing-remitting multiple-sclerosis
title_sort safety and persistence of dimethyl fumarate as a treatment for relapsing remitting multiple sclerosis
topic dimethyl fumarate
relapsing remitting multiple sclerosis
drug safety
lymphopenia
adverse drug events
toxicity
url http://www.aulamedica.es/fh/pdf/11567.pdf
work_keys_str_mv AT silviaboullosalale safetyandpersistenceofdimethylfumarateasatreatmentforrelapsingremittingmultiplesclerosis
AT laragonzalezfreire safetyandpersistenceofdimethylfumarateasatreatmentforrelapsingremittingmultiplesclerosis
AT lucianomartinezmartinez safetyandpersistenceofdimethylfumarateasatreatmentforrelapsingremittingmultiplesclerosis
AT carloscrespodiz safetyandpersistenceofdimethylfumarateasatreatmentforrelapsingremittingmultiplesclerosis