Advances in Nucleic Acid Drugs and Gene Therapies based on Animal Models of Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a severe X-linked recessive genetic disorder caused by mutations in the DMD gene, making it one of the most common forms of hereditary muscular dystrophy. The DMD gene, which encodes dystrophin, is the largest known gene in the human genome. Mutations in the DMD...
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Main Authors: | LIU Siyu, LAI Yuezhao, GUO Wenting, CHEN Xuejin |
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Format: | Article |
Language: | zho |
Published: |
Editorial Office of Laboratory Animal and Comparative Medicine
2024-12-01
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Series: | Shiyan dongwu yu bijiao yixue |
Subjects: | |
Online Access: | https://www.slarc.org.cn/dwyx/CN/10.12300/j.issn.1674-5817.2024.168 |
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