Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap

In Periodic Paralysis (PP), a rare inherited condition caused by mutation in skeletal muscle ion channels, the phenotype changes with age, transitioning from the episodic attacks of weakness that give the condition its name, to a more degenerative phenotype of permanent progressive weakness and myop...

Full description

Saved in:
Bibliographic Details
Main Authors: Karen Suetterlin, Sinead Law, William David Arnold
Format: Article
Language:English
Published: Frontiers Media S.A. 2024-12-01
Series:Frontiers in Neurology
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fneur.2024.1507485/full
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1846110247559626752
author Karen Suetterlin
Karen Suetterlin
Sinead Law
William David Arnold
William David Arnold
William David Arnold
William David Arnold
author_facet Karen Suetterlin
Karen Suetterlin
Sinead Law
William David Arnold
William David Arnold
William David Arnold
William David Arnold
author_sort Karen Suetterlin
collection DOAJ
description In Periodic Paralysis (PP), a rare inherited condition caused by mutation in skeletal muscle ion channels, the phenotype changes with age, transitioning from the episodic attacks of weakness that give the condition its name, to a more degenerative phenotype of permanent progressive weakness and myopathy. This leads to disability and reduced quality of life. Neither the cause of this phenotype transition, nor why it occurs around the age of 40 is known. However, 40 is also the age of onset of ‘normal’ age-related physiological decline when we consider (a) muscle mass and strength (b) physical function at the world class level and (c) age-related mitochondrial dysfunction. Elevated Na+, mitochondrial dysfunction and sarcoplasmic Ca2+ leak via the skeletal muscle ryanodine receptor (RyR1) have been implicated in both periodic paralysis myopathy and skeletal muscle ageing. We suggest this combination may trigger a negative spiral ultimately leading to progressive muscle failure. Understanding the interaction between ageing physiology and disease phenotype will provide a window into the healthy ageing process but also help understand how, and why PP phenotype changes with age. Understanding the mechanism underlying PP phenotype-transition and its link with ageing physiology, not only has the potential to identify the first disease modifying therapies for PP, but also to identify novel and potentially tractable mechanisms that contribute to sarcopenia, the pathological loss of muscle mass and function with age.
format Article
id doaj-art-5709a4c4c3624e539de7d3ecad7916aa
institution Kabale University
issn 1664-2295
language English
publishDate 2024-12-01
publisher Frontiers Media S.A.
record_format Article
series Frontiers in Neurology
spelling doaj-art-5709a4c4c3624e539de7d3ecad7916aa2024-12-24T10:04:03ZengFrontiers Media S.A.Frontiers in Neurology1664-22952024-12-011510.3389/fneur.2024.15074851507485Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlapKaren Suetterlin0Karen Suetterlin1Sinead Law2William David Arnold3William David Arnold4William David Arnold5William David Arnold6AGE Research Group, NIHR Newcastle Biomedical Research Centre, Newcastle Upon Tyne Hospitals NHS Foundation Trust, Cumbria, Northumberland, Tyne and Wear NHS Foundation Trust and Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United KingdomThe John Walton Muscular Dystrophy Research Centre, Institute of Genetic Medicine, Newcastle upon Tyne, United KingdomAGE Research Group, NIHR Newcastle Biomedical Research Centre, Newcastle Upon Tyne Hospitals NHS Foundation Trust, Cumbria, Northumberland, Tyne and Wear NHS Foundation Trust and Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United KingdomNextGen Precision Health, University of Missouri, Columbia, MO, United StatesDepartment of Physical Medicine and Rehabilitation, University of Missouri, Columbia, MO, United StatesDepartment of Medical Pharmacology and Physiology, University of Missouri, Columbia, MO, United StatesDepartment of Neurology, University of Missouri, Columbia, MO, United StatesIn Periodic Paralysis (PP), a rare inherited condition caused by mutation in skeletal muscle ion channels, the phenotype changes with age, transitioning from the episodic attacks of weakness that give the condition its name, to a more degenerative phenotype of permanent progressive weakness and myopathy. This leads to disability and reduced quality of life. Neither the cause of this phenotype transition, nor why it occurs around the age of 40 is known. However, 40 is also the age of onset of ‘normal’ age-related physiological decline when we consider (a) muscle mass and strength (b) physical function at the world class level and (c) age-related mitochondrial dysfunction. Elevated Na+, mitochondrial dysfunction and sarcoplasmic Ca2+ leak via the skeletal muscle ryanodine receptor (RyR1) have been implicated in both periodic paralysis myopathy and skeletal muscle ageing. We suggest this combination may trigger a negative spiral ultimately leading to progressive muscle failure. Understanding the interaction between ageing physiology and disease phenotype will provide a window into the healthy ageing process but also help understand how, and why PP phenotype changes with age. Understanding the mechanism underlying PP phenotype-transition and its link with ageing physiology, not only has the potential to identify the first disease modifying therapies for PP, but also to identify novel and potentially tractable mechanisms that contribute to sarcopenia, the pathological loss of muscle mass and function with age.https://www.frontiersin.org/articles/10.3389/fneur.2024.1507485/fullageingmyopathysarcopeniachannelopathylife coursemitochondria
spellingShingle Karen Suetterlin
Karen Suetterlin
Sinead Law
William David Arnold
William David Arnold
William David Arnold
William David Arnold
Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
Frontiers in Neurology
ageing
myopathy
sarcopenia
channelopathy
life course
mitochondria
title Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
title_full Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
title_fullStr Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
title_full_unstemmed Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
title_short Periodic paralysis across the life course: age-related phenotype transition and sarcopenia overlap
title_sort periodic paralysis across the life course age related phenotype transition and sarcopenia overlap
topic ageing
myopathy
sarcopenia
channelopathy
life course
mitochondria
url https://www.frontiersin.org/articles/10.3389/fneur.2024.1507485/full
work_keys_str_mv AT karensuetterlin periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT karensuetterlin periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT sineadlaw periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT williamdavidarnold periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT williamdavidarnold periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT williamdavidarnold periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap
AT williamdavidarnold periodicparalysisacrossthelifecourseagerelatedphenotypetransitionandsarcopeniaoverlap