Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population

ABSTRACT Background Newborn screening (NBS) for isovaleric acidemia (IVA) is implemented via tandem mass spectrometry (MS/MS), but false‐positive results are still common. In addition, NBS for IVA is limited by a lack of suitable biomarkers, especially after the use of pivaloylester‐containing antib...

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Main Authors: Wei Zhou, Ting Huang, Huizhong Li, Maosheng Gu
Format: Article
Language:English
Published: Wiley 2024-11-01
Series:Molecular Genetics & Genomic Medicine
Subjects:
Online Access:https://doi.org/10.1002/mgg3.70034
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author Wei Zhou
Ting Huang
Huizhong Li
Maosheng Gu
author_facet Wei Zhou
Ting Huang
Huizhong Li
Maosheng Gu
author_sort Wei Zhou
collection DOAJ
description ABSTRACT Background Newborn screening (NBS) for isovaleric acidemia (IVA) is implemented via tandem mass spectrometry (MS/MS), but false‐positive results are still common. In addition, NBS for IVA is limited by a lack of suitable biomarkers, especially after the use of pivaloylester‐containing antibiotics. Methods We conducted a retrospective cohort study to explore the clinical correlation between antibiotic administration and false‐positive results for isovalerylcarnitine (C5). Results A total of 509,313 newborns were recruited from the initial NBS study, only one of whom underwent genetic confirmation, conducted between 2015 and 2020. Significant associations between false‐positive C5‐carnitine screening results and treatment with pivalate‐generating antibiotics were identified with retrospective analysis. Conclusions The current results highlight the detrimental effects of false‐positive C5‐carnitine screening results. Unless the licensing of pivalate‐generating antibiotics for use during the neonatal period is reconsidered, a second‐tier test for C5 determination will be necessary.
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spelling doaj-art-3865d79603d348509ff5d8bfeb4e1fe82024-11-27T06:54:36ZengWileyMolecular Genetics & Genomic Medicine2324-92692024-11-011211n/an/a10.1002/mgg3.70034Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese PopulationWei Zhou0Ting Huang1Huizhong Li2Maosheng Gu3Neonatal Screening Center Xuzhou Maternity and Child Health Care Hospital Xuzhou Jiangsu ChinaDepartment of Pharmacy Xuzhou Maternity and Child Health Care Hospital Xuzhou Jiangsu ChinaNeonatal Screening Center Xuzhou Maternity and Child Health Care Hospital Xuzhou Jiangsu ChinaNeonatal Screening Center Xuzhou Maternity and Child Health Care Hospital Xuzhou Jiangsu ChinaABSTRACT Background Newborn screening (NBS) for isovaleric acidemia (IVA) is implemented via tandem mass spectrometry (MS/MS), but false‐positive results are still common. In addition, NBS for IVA is limited by a lack of suitable biomarkers, especially after the use of pivaloylester‐containing antibiotics. Methods We conducted a retrospective cohort study to explore the clinical correlation between antibiotic administration and false‐positive results for isovalerylcarnitine (C5). Results A total of 509,313 newborns were recruited from the initial NBS study, only one of whom underwent genetic confirmation, conducted between 2015 and 2020. Significant associations between false‐positive C5‐carnitine screening results and treatment with pivalate‐generating antibiotics were identified with retrospective analysis. Conclusions The current results highlight the detrimental effects of false‐positive C5‐carnitine screening results. Unless the licensing of pivalate‐generating antibiotics for use during the neonatal period is reconsidered, a second‐tier test for C5 determination will be necessary.https://doi.org/10.1002/mgg3.70034isovaleric acidemiapivalate‐generating antibioticssecond‐tier screening
spellingShingle Wei Zhou
Ting Huang
Huizhong Li
Maosheng Gu
Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
Molecular Genetics & Genomic Medicine
isovaleric acidemia
pivalate‐generating antibiotics
second‐tier screening
title Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
title_full Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
title_fullStr Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
title_full_unstemmed Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
title_short Newborn Screening for Isovaleric Acidemia: Treatment With Pivalate‐Generating Antibiotics Contributed to False C5‐Carnitine Positivity in a Chinese Population
title_sort newborn screening for isovaleric acidemia treatment with pivalate generating antibiotics contributed to false c5 carnitine positivity in a chinese population
topic isovaleric acidemia
pivalate‐generating antibiotics
second‐tier screening
url https://doi.org/10.1002/mgg3.70034
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