Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation

Parkin (PRKN) is recognized as causative gene in early-onset Parkinson’s disease (PD). Induced pluripotent stem cells (iPSCs) were derived from a 29-year-old PD patient carrying a heterozygous c.823C > T (p.R275W) variant and an exon 2–4 deletion in PRKN. The Generated iPSCs maintain a normal kar...

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Main Authors: Jingke Cheng, Yingtong Zhai, Xiangge Guo, Xumeng Wang, Min Ma, Xin Ren, Shan Wang, Huixian Cui, Qian Ren
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Stem Cell Research
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506124002769
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author Jingke Cheng
Yingtong Zhai
Xiangge Guo
Xumeng Wang
Min Ma
Xin Ren
Shan Wang
Huixian Cui
Qian Ren
author_facet Jingke Cheng
Yingtong Zhai
Xiangge Guo
Xumeng Wang
Min Ma
Xin Ren
Shan Wang
Huixian Cui
Qian Ren
author_sort Jingke Cheng
collection DOAJ
description Parkin (PRKN) is recognized as causative gene in early-onset Parkinson’s disease (PD). Induced pluripotent stem cells (iPSCs) were derived from a 29-year-old PD patient carrying a heterozygous c.823C > T (p.R275W) variant and an exon 2–4 deletion in PRKN. The Generated iPSCs maintain a normal karyotype, express pluripotency markers, and retain the ability to differentiate into the three germ layers. This iPSC line serves as a valuable cellular model for investigating the pathogenesis of early-onset PD and development of potential therapeutic interventions.
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institution Kabale University
issn 1873-5061
language English
publishDate 2024-12-01
publisher Elsevier
record_format Article
series Stem Cell Research
spelling doaj-art-34d686f3d1064b0abb11e80fbbd57b8b2024-12-13T10:56:52ZengElsevierStem Cell Research1873-50612024-12-0181103578Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutationJingke Cheng0Yingtong Zhai1Xiangge Guo2Xumeng Wang3Min Ma4Xin Ren5Shan Wang6Huixian Cui7Qian Ren8Department of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, ChinaDepartment of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, ChinaDepartment of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, ChinaDepartment of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, ChinaDepartment of Human Anatomy, Hebei Medical University, Shijiazhuang, China; Human Brain Bank, Hebei Medical University, Shijiazhuang, ChinaDepartment of Neurology, The Second Hospital of Hebei Medical University, Shijiazhuang, ChinaDepartment of Neurology, The Second Hospital of Hebei Medical University, Shijiazhuang, ChinaDepartment of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, China; Hebei Key Laboratory of Neurodegenerative Disease Mechanism, Hebei Medical University, Shijiazhuang, China; Corresponding authors.Department of Human Anatomy, Hebei Medical University, Shijiazhuang, China; International Cooperation Laboratory of Stem Cell Research, Hebei Medical University, Shijiazhuang, China; Hebei Key Laboratory of Neurodegenerative Disease Mechanism, Hebei Medical University, Shijiazhuang, China; The Key Laboratory of Neural and Vascular Biology, Ministry of Education, Shijiazhuang, China; Corresponding authors.Parkin (PRKN) is recognized as causative gene in early-onset Parkinson’s disease (PD). Induced pluripotent stem cells (iPSCs) were derived from a 29-year-old PD patient carrying a heterozygous c.823C > T (p.R275W) variant and an exon 2–4 deletion in PRKN. The Generated iPSCs maintain a normal karyotype, express pluripotency markers, and retain the ability to differentiate into the three germ layers. This iPSC line serves as a valuable cellular model for investigating the pathogenesis of early-onset PD and development of potential therapeutic interventions.http://www.sciencedirect.com/science/article/pii/S1873506124002769
spellingShingle Jingke Cheng
Yingtong Zhai
Xiangge Guo
Xumeng Wang
Min Ma
Xin Ren
Shan Wang
Huixian Cui
Qian Ren
Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
Stem Cell Research
title Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
title_full Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
title_fullStr Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
title_full_unstemmed Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
title_short Generation of an induced pluripotent stem cell line (HMSCATi004-A) from an early onset Parkinson’s disease patient with PRKN gene mutation
title_sort generation of an induced pluripotent stem cell line hmscati004 a from an early onset parkinson s disease patient with prkn gene mutation
url http://www.sciencedirect.com/science/article/pii/S1873506124002769
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