Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder

We present a 7-year-old girl who presented to our emergency department in active status epilepticus. Seizures responded to standard antiepileptic medications; however, baseline work-up for seizure etiology remained unremarkable. Her new-onset seizures were further investigated via EEG and MRI brain...

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Main Authors: Fatima Farid Mir, Mohammad Ashraf
Format: Article
Language:English
Published: Knowledge E 2024-10-01
Series:Dubai Medical Journal
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Online Access:https://www.knepublishing.com/index.php/DMJ/article/view/17494
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author Fatima Farid Mir
Mohammad Ashraf
author_facet Fatima Farid Mir
Mohammad Ashraf
author_sort Fatima Farid Mir
collection DOAJ
description We present a 7-year-old girl who presented to our emergency department in active status epilepticus. Seizures responded to standard antiepileptic medications; however, baseline work-up for seizure etiology remained unremarkable. Her new-onset seizures were further investigated via EEG and MRI brain, which revealed focal epileptiform discharges and periventricular nodular heterotopia, respectively. Concurrently, the clinical evaluation revealed extensive marfanoid features, and a personal history of eczema and asthma. Her family history was pertinent for aortic valve disease, asthma, and tall stature. Given the peculiar skeletal features, allergic propensities and coexistent weighty family history, a molecular genetic panel analysis for Marfan Syndrome and Loeys-Dietz Syndrome (LDS) were sought. Genetic testing revealed an underlying heterozygous variant in the TGFBR-1 gene; thereby confirming the presence of LDS. The child had responded well to single antiepileptic agent therapy and was discharged in good condition with regular outpatient cardiac and neurology follow-up. This is a unique case reported of a child with genetically diagnosed LDS concurring with an underlying neuronal migration disorder, manifesting in an acute, severe, and lifethreatening fashion.
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spelling doaj-art-2e9786a2126d4268aa9ef7d92c1d18c82024-11-25T10:24:54ZengKnowledge EDubai Medical Journal2571-726X2024-10-017110.18502/dmj.v7i1.17494Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration DisorderFatima Farid Mir0Mohammad Ashraf1Pediatric Department, Dubai Hospital, DubaiPediatric Department, Dubai Hospital, Dubai We present a 7-year-old girl who presented to our emergency department in active status epilepticus. Seizures responded to standard antiepileptic medications; however, baseline work-up for seizure etiology remained unremarkable. Her new-onset seizures were further investigated via EEG and MRI brain, which revealed focal epileptiform discharges and periventricular nodular heterotopia, respectively. Concurrently, the clinical evaluation revealed extensive marfanoid features, and a personal history of eczema and asthma. Her family history was pertinent for aortic valve disease, asthma, and tall stature. Given the peculiar skeletal features, allergic propensities and coexistent weighty family history, a molecular genetic panel analysis for Marfan Syndrome and Loeys-Dietz Syndrome (LDS) were sought. Genetic testing revealed an underlying heterozygous variant in the TGFBR-1 gene; thereby confirming the presence of LDS. The child had responded well to single antiepileptic agent therapy and was discharged in good condition with regular outpatient cardiac and neurology follow-up. This is a unique case reported of a child with genetically diagnosed LDS concurring with an underlying neuronal migration disorder, manifesting in an acute, severe, and lifethreatening fashion. https://www.knepublishing.com/index.php/DMJ/article/view/17494epilepsyLoeys-Dietz Syndromeneuronal migration disorderseizures
spellingShingle Fatima Farid Mir
Mohammad Ashraf
Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
Dubai Medical Journal
epilepsy
Loeys-Dietz Syndrome
neuronal migration disorder
seizures
title Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
title_full Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
title_fullStr Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
title_full_unstemmed Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
title_short Epilepsy in Loeys-Dietz Syndrome: The Rare Concurrence of a Connective Tissue and Neuronal Migration Disorder
title_sort epilepsy in loeys dietz syndrome the rare concurrence of a connective tissue and neuronal migration disorder
topic epilepsy
Loeys-Dietz Syndrome
neuronal migration disorder
seizures
url https://www.knepublishing.com/index.php/DMJ/article/view/17494
work_keys_str_mv AT fatimafaridmir epilepsyinloeysdietzsyndrometherareconcurrenceofaconnectivetissueandneuronalmigrationdisorder
AT mohammadashraf epilepsyinloeysdietzsyndrometherareconcurrenceofaconnectivetissueandneuronalmigrationdisorder