Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment

Abstract Introduction Treatment options for Waldenström's Macroglobulinemia (WM) have expanded rapidly in the last decades. However, there is no consensus on a preferred treatment. Therefore, patient preferences become increasingly important in making individualized treatment plans. Still, WM p...

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Main Authors: Karima Amaador, Pythia T. Nieuwkerk, Monique C. Minnema, Marie José Kersten, Josephine M. I. Vos
Format: Article
Language:English
Published: Wiley 2023-02-01
Series:Cancer Medicine
Subjects:
Online Access:https://doi.org/10.1002/cam4.5080
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author Karima Amaador
Pythia T. Nieuwkerk
Monique C. Minnema
Marie José Kersten
Josephine M. I. Vos
author_facet Karima Amaador
Pythia T. Nieuwkerk
Monique C. Minnema
Marie José Kersten
Josephine M. I. Vos
author_sort Karima Amaador
collection DOAJ
description Abstract Introduction Treatment options for Waldenström's Macroglobulinemia (WM) have expanded rapidly in the last decades. However, there is no consensus on a preferred treatment. Therefore, patient preferences become increasingly important in making individualized treatment plans. Still, WM patients' priorities and perspectives regarding their treatment options are unknown. We evaluated treatment preferences of WM patients using a discrete choice experiment (DCE). Methods A mixed‐method approach was utilized for identification and selection of attributes/levels. The DCE questionnaire included five attributes: type of agent (targeted versus chemotherapy); frequency and route of administration; 5‐year progression‐free survival (PFS); adverse events; and risk of secondary malignancies. An orthogonal design and a mixed logit panel data model were used to construct choice tasks and assess patient preferences, respectively. Results Three hundred thirty WM patients participated in the project. In total, 214 (65%) complete questionnaires were included for data analysis. The 5‐year PFS, followed by risk of secondary malignancies were the most important attributes for making treatment choices. Regarding side effects, patients chose to avoid neuropathy the most compared to nausea/vomiting and extreme fatigue. Patients preferred a fixed‐duration treatment with IV/SC administration at the hospital over a continuous daily oral regimen at home. Conclusion These are the first systematic data obtained on WM patient preferences for treatment. The results may help discussions with individual patients about their treatment choices. Also, these data can help design clinical trials in WM and inform health‐care decision‐making regarding outcomes that are most relevant to patients.
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spelling doaj-art-1f3f15c7d1d242fcb3c1a501b8d78c1e2024-11-25T07:56:32ZengWileyCancer Medicine2045-76342023-02-011233376338610.1002/cam4.5080Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experimentKarima Amaador0Pythia T. Nieuwkerk1Monique C. Minnema2Marie José Kersten3Josephine M. I. Vos4Amsterdam UMC, University of Amsterdam, Department of Hematology Cancer Center Amsterdam Amsterdam The NetherlandsDepartment of Medical Psychology Academic Medical Center Amsterdam The NetherlandsDepartment of Hematology, University Medical Center Utrecht University Utrecht Utrecht The NetherlandsAmsterdam UMC, University of Amsterdam, Department of Hematology Cancer Center Amsterdam Amsterdam The NetherlandsAmsterdam UMC, University of Amsterdam, Department of Hematology Cancer Center Amsterdam Amsterdam The NetherlandsAbstract Introduction Treatment options for Waldenström's Macroglobulinemia (WM) have expanded rapidly in the last decades. However, there is no consensus on a preferred treatment. Therefore, patient preferences become increasingly important in making individualized treatment plans. Still, WM patients' priorities and perspectives regarding their treatment options are unknown. We evaluated treatment preferences of WM patients using a discrete choice experiment (DCE). Methods A mixed‐method approach was utilized for identification and selection of attributes/levels. The DCE questionnaire included five attributes: type of agent (targeted versus chemotherapy); frequency and route of administration; 5‐year progression‐free survival (PFS); adverse events; and risk of secondary malignancies. An orthogonal design and a mixed logit panel data model were used to construct choice tasks and assess patient preferences, respectively. Results Three hundred thirty WM patients participated in the project. In total, 214 (65%) complete questionnaires were included for data analysis. The 5‐year PFS, followed by risk of secondary malignancies were the most important attributes for making treatment choices. Regarding side effects, patients chose to avoid neuropathy the most compared to nausea/vomiting and extreme fatigue. Patients preferred a fixed‐duration treatment with IV/SC administration at the hospital over a continuous daily oral regimen at home. Conclusion These are the first systematic data obtained on WM patient preferences for treatment. The results may help discussions with individual patients about their treatment choices. Also, these data can help design clinical trials in WM and inform health‐care decision‐making regarding outcomes that are most relevant to patients.https://doi.org/10.1002/cam4.5080discrete choice experimentmacroglobulinemiapatient preferenceswaldenstrom's
spellingShingle Karima Amaador
Pythia T. Nieuwkerk
Monique C. Minnema
Marie José Kersten
Josephine M. I. Vos
Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
Cancer Medicine
discrete choice experiment
macroglobulinemia
patient preferences
waldenstrom's
title Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
title_full Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
title_fullStr Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
title_full_unstemmed Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
title_short Patient preferences regarding treatment options for Waldenström's macroglobulinemia: A discrete choice experiment
title_sort patient preferences regarding treatment options for waldenstrom s macroglobulinemia a discrete choice experiment
topic discrete choice experiment
macroglobulinemia
patient preferences
waldenstrom's
url https://doi.org/10.1002/cam4.5080
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