EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)

The article is dedicated to modern approaches to treatment of Gaucher’s disease. The authors list the primary aspects of the disease and present data on the origin and introduction of pathogenetic enzyme replacement therapy to clinical practice. Review of international clinical studies demonstrates...

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Main Authors: O. S. Gundobina, G. B. Movsisyan, E. V. Komarova, L. S. Namazova-Baranova
Format: Article
Language:Russian
Published: Union of pediatricians of Russia 2014-11-01
Series:Педиатрическая фармакология
Subjects:
Online Access:https://www.pedpharma.ru/jour/article/view/35
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author O. S. Gundobina
G. B. Movsisyan
E. V. Komarova
L. S. Namazova-Baranova
author_facet O. S. Gundobina
G. B. Movsisyan
E. V. Komarova
L. S. Namazova-Baranova
author_sort O. S. Gundobina
collection DOAJ
description The article is dedicated to modern approaches to treatment of Gaucher’s disease. The authors list the primary aspects of the disease and present data on the origin and introduction of pathogenetic enzyme replacement therapy to clinical practice. Review of international clinical studies demonstrates high effectiveness and safety of long-term enzyme replacement therapy with velaglucerase alfa in patients with confirmed type I Gaucher’s disease.
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institution Kabale University
issn 1727-5776
2500-3089
language Russian
publishDate 2014-11-01
publisher Union of pediatricians of Russia
record_format Article
series Педиатрическая фармакология
spelling doaj-art-1d41a926b6ae4c4fbb45279bccaa463f2025-08-20T03:59:16ZrusUnion of pediatricians of RussiaПедиатрическая фармакология1727-57762500-30892014-11-01116525510.15690/pf.v11i6.121535EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)O. S. Gundobina0G. B. Movsisyan1E. V. Komarova2L. S. Namazova-Baranova3Scientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationScientific Center of Children’s Health, Moscow, Russian FederationThe article is dedicated to modern approaches to treatment of Gaucher’s disease. The authors list the primary aspects of the disease and present data on the origin and introduction of pathogenetic enzyme replacement therapy to clinical practice. Review of international clinical studies demonstrates high effectiveness and safety of long-term enzyme replacement therapy with velaglucerase alfa in patients with confirmed type I Gaucher’s disease.https://www.pedpharma.ru/jour/article/view/35gaucher’s diseaseenzyme replacement therapyvelaglucerase alfachildren
spellingShingle O. S. Gundobina
G. B. Movsisyan
E. V. Komarova
L. S. Namazova-Baranova
EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
Педиатрическая фармакология
gaucher’s disease
enzyme replacement therapy
velaglucerase alfa
children
title EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
title_full EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
title_fullStr EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
title_full_unstemmed EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
title_short EFFECTIVENESS AND SAFETY OF VELAGLUCERASE ALFA IN TREATMENT OF GAUCHER DISEASE TYPE 1 (ACCORDING TO INTERNATIONAL STUDIES)
title_sort effectiveness and safety of velaglucerase alfa in treatment of gaucher disease type 1 according to international studies
topic gaucher’s disease
enzyme replacement therapy
velaglucerase alfa
children
url https://www.pedpharma.ru/jour/article/view/35
work_keys_str_mv AT osgundobina effectivenessandsafetyofvelaglucerasealfaintreatmentofgaucherdiseasetype1accordingtointernationalstudies
AT gbmovsisyan effectivenessandsafetyofvelaglucerasealfaintreatmentofgaucherdiseasetype1accordingtointernationalstudies
AT evkomarova effectivenessandsafetyofvelaglucerasealfaintreatmentofgaucherdiseasetype1accordingtointernationalstudies
AT lsnamazovabaranova effectivenessandsafetyofvelaglucerasealfaintreatmentofgaucherdiseasetype1accordingtointernationalstudies