Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease

Abstract Treatment with L-3,4-dihydroxyphenylalanine (L-Dopa) compensates for decreased striatal dopamine (DA) levels and reduces Parkinson’s disease (PD) symptoms. However, during disease progression, L-Dopa-induced dyskinesia (LID) develops virtually in all PD patients, making the control of PD sy...

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Main Authors: Federica Servillo, Maria De Carluccio, Giulia Di Lazzaro, Federica Campanelli, Gioia Marino, Giuseppina Natale, Ada Ledonne, Mariangela Massaro Cenere, Emanuela Paldino, Daniela Di Giuda, Anna Picca, Francesco Bove, Riccardo Di Iorio, Benedetta Angeloni, Angelo Tiziano Cimmino, Giovanni Bellomo, Barbara Picconi, Anna Rita Bentivoglio, Nicola Biagio Mercuri, Lucilla Parnetti, Veronica Ghiglieri, Maria Teresa Viscomi, Paolo Calabresi
Format: Article
Language:English
Published: Nature Portfolio 2024-11-01
Series:npj Parkinson's Disease
Online Access:https://doi.org/10.1038/s41531-024-00836-6
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author Federica Servillo
Maria De Carluccio
Giulia Di Lazzaro
Federica Campanelli
Gioia Marino
Giuseppina Natale
Ada Ledonne
Mariangela Massaro Cenere
Emanuela Paldino
Daniela Di Giuda
Anna Picca
Francesco Bove
Riccardo Di Iorio
Benedetta Angeloni
Angelo Tiziano Cimmino
Giovanni Bellomo
Barbara Picconi
Anna Rita Bentivoglio
Nicola Biagio Mercuri
Lucilla Parnetti
Veronica Ghiglieri
Maria Teresa Viscomi
Paolo Calabresi
author_facet Federica Servillo
Maria De Carluccio
Giulia Di Lazzaro
Federica Campanelli
Gioia Marino
Giuseppina Natale
Ada Ledonne
Mariangela Massaro Cenere
Emanuela Paldino
Daniela Di Giuda
Anna Picca
Francesco Bove
Riccardo Di Iorio
Benedetta Angeloni
Angelo Tiziano Cimmino
Giovanni Bellomo
Barbara Picconi
Anna Rita Bentivoglio
Nicola Biagio Mercuri
Lucilla Parnetti
Veronica Ghiglieri
Maria Teresa Viscomi
Paolo Calabresi
author_sort Federica Servillo
collection DOAJ
description Abstract Treatment with L-3,4-dihydroxyphenylalanine (L-Dopa) compensates for decreased striatal dopamine (DA) levels and reduces Parkinson’s disease (PD) symptoms. However, during disease progression, L-Dopa-induced dyskinesia (LID) develops virtually in all PD patients, making the control of PD symptoms difficult. Thus, understanding the mechanisms underlying LID and the control of these motor abnormalities is a major issue in the care of PD patients. From experimental and clinical studies, a complex cascade of molecular and cellular events emerges, but the primary determinants of LID are still unclear. Here, with a translational approach, including four animal models and a wide cohort of PD patients, we show that striatal DA denervation is the major causal factor for the emergence of LID, while α-synuclein aggregates do not seem to play a significant role. Our data also support the concept that maladaptive basal ganglia plasticity is the main pathophysiological mechanism underlying LID.
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spelling doaj-art-15139aaebfe7489f9dcd055e7b51e20c2024-12-01T12:15:04ZengNature Portfolionpj Parkinson's Disease2373-80572024-11-0110111310.1038/s41531-024-00836-6Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s DiseaseFederica Servillo0Maria De Carluccio1Giulia Di Lazzaro2Federica Campanelli3Gioia Marino4Giuseppina Natale5Ada Ledonne6Mariangela Massaro Cenere7Emanuela Paldino8Daniela Di Giuda9Anna Picca10Francesco Bove11Riccardo Di Iorio12Benedetta Angeloni13Angelo Tiziano Cimmino14Giovanni Bellomo15Barbara Picconi16Anna Rita Bentivoglio17Nicola Biagio Mercuri18Lucilla Parnetti19Veronica Ghiglieri20Maria Teresa Viscomi21Paolo Calabresi22Neurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeuroscienze Sperimentali, IRCCS Fondazione Santa LuciaNeuroscienze Sperimentali, IRCCS Fondazione Santa LuciaNeuroscienze Sperimentali, IRCCS Fondazione Santa LuciaMedicina Nucleare, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSLaboratorio di Neurochimica Clinica, Neurologia, Dipartimento di Medicina, Università degli Studi di PerugiaDipartimento di Scienze Umane e Promozione della Qualità della Vita, Università Telematica San RaffaeleNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeuroscienze Sperimentali, IRCCS Fondazione Santa LuciaLaboratorio di Neurochimica Clinica, Neurologia, Dipartimento di Medicina, Università degli Studi di PerugiaNeurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCSNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreNeurologia, Dipartimento di Neuroscienze, Università Cattolica del Sacro CuoreAbstract Treatment with L-3,4-dihydroxyphenylalanine (L-Dopa) compensates for decreased striatal dopamine (DA) levels and reduces Parkinson’s disease (PD) symptoms. However, during disease progression, L-Dopa-induced dyskinesia (LID) develops virtually in all PD patients, making the control of PD symptoms difficult. Thus, understanding the mechanisms underlying LID and the control of these motor abnormalities is a major issue in the care of PD patients. From experimental and clinical studies, a complex cascade of molecular and cellular events emerges, but the primary determinants of LID are still unclear. Here, with a translational approach, including four animal models and a wide cohort of PD patients, we show that striatal DA denervation is the major causal factor for the emergence of LID, while α-synuclein aggregates do not seem to play a significant role. Our data also support the concept that maladaptive basal ganglia plasticity is the main pathophysiological mechanism underlying LID.https://doi.org/10.1038/s41531-024-00836-6
spellingShingle Federica Servillo
Maria De Carluccio
Giulia Di Lazzaro
Federica Campanelli
Gioia Marino
Giuseppina Natale
Ada Ledonne
Mariangela Massaro Cenere
Emanuela Paldino
Daniela Di Giuda
Anna Picca
Francesco Bove
Riccardo Di Iorio
Benedetta Angeloni
Angelo Tiziano Cimmino
Giovanni Bellomo
Barbara Picconi
Anna Rita Bentivoglio
Nicola Biagio Mercuri
Lucilla Parnetti
Veronica Ghiglieri
Maria Teresa Viscomi
Paolo Calabresi
Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
npj Parkinson's Disease
title Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
title_full Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
title_fullStr Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
title_full_unstemmed Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
title_short Molecular and cellular determinants of L-Dopa-induced dyskinesia in Parkinson’s Disease
title_sort molecular and cellular determinants of l dopa induced dyskinesia in parkinson s disease
url https://doi.org/10.1038/s41531-024-00836-6
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