A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors

Summary: Inflammasomes are protein complexes that mediate innate immune responses whose dysregulation has been linked to a spectrum of acute and chronic human conditions, which dictates therapeutic development that is aligned with disease variability. We designed a scalable, physiologic high-content...

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Main Authors: Daniel Chen, Tempest Plott, Michael Wiest, Will Van Trump, Ben Komalo, Dat Nguyen, Charlie Marsh, Jarred Heinrich, Colin J. Fuller, Lauren Nicolaisen, Elisa Cambronero, An Nguyen, Christian Elabd, Francesco Rubbo, Rachel DeVay Jacobson
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Language:English
Published: Elsevier 2024-12-01
Series:iScience
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Online Access:http://www.sciencedirect.com/science/article/pii/S2589004224026294
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author Daniel Chen
Tempest Plott
Michael Wiest
Will Van Trump
Ben Komalo
Dat Nguyen
Charlie Marsh
Jarred Heinrich
Colin J. Fuller
Lauren Nicolaisen
Elisa Cambronero
An Nguyen
Christian Elabd
Francesco Rubbo
Rachel DeVay Jacobson
author_facet Daniel Chen
Tempest Plott
Michael Wiest
Will Van Trump
Ben Komalo
Dat Nguyen
Charlie Marsh
Jarred Heinrich
Colin J. Fuller
Lauren Nicolaisen
Elisa Cambronero
An Nguyen
Christian Elabd
Francesco Rubbo
Rachel DeVay Jacobson
author_sort Daniel Chen
collection DOAJ
description Summary: Inflammasomes are protein complexes that mediate innate immune responses whose dysregulation has been linked to a spectrum of acute and chronic human conditions, which dictates therapeutic development that is aligned with disease variability. We designed a scalable, physiologic high-content imaging assay in human PBMCs that we analyzed using a combination of machine-learning and cell biology methods. This resulted in a set of biologically interpretable readouts that can resolve a spectrum of cellular states associated with inflammasome activation and inhibition. These methods were applied to a phenotypic screen that surfaced mechanistically distinct inflammasome inhibitors from an annotated 12,000 compound library. A set of over 100 inhibitors, including an array of Raf-pathway inhibitors, were validated in downstream functional assays. This approach demonstrates how complementary machine learning-based methods can be used to generate profiles of cellular states associated with different stages of complex biological pathways and yield compound and target discovery.
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institution Kabale University
issn 2589-0042
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publishDate 2024-12-01
publisher Elsevier
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series iScience
spelling doaj-art-01cb3490251649b8b5df12f29f5f035a2024-12-22T05:29:15ZengElsevieriScience2589-00422024-12-012712111404A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitorsDaniel Chen0Tempest Plott1Michael Wiest2Will Van Trump3Ben Komalo4Dat Nguyen5Charlie Marsh6Jarred Heinrich7Colin J. Fuller8Lauren Nicolaisen9Elisa Cambronero10An Nguyen11Christian Elabd12Francesco Rubbo13Rachel DeVay Jacobson14Spring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USASpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USA; Corresponding authorSpring Discovery, Inc., 1125 Industrial Road, San Carlos, CA 94070, USA; Corresponding authorSummary: Inflammasomes are protein complexes that mediate innate immune responses whose dysregulation has been linked to a spectrum of acute and chronic human conditions, which dictates therapeutic development that is aligned with disease variability. We designed a scalable, physiologic high-content imaging assay in human PBMCs that we analyzed using a combination of machine-learning and cell biology methods. This resulted in a set of biologically interpretable readouts that can resolve a spectrum of cellular states associated with inflammasome activation and inhibition. These methods were applied to a phenotypic screen that surfaced mechanistically distinct inflammasome inhibitors from an annotated 12,000 compound library. A set of over 100 inhibitors, including an array of Raf-pathway inhibitors, were validated in downstream functional assays. This approach demonstrates how complementary machine learning-based methods can be used to generate profiles of cellular states associated with different stages of complex biological pathways and yield compound and target discovery.http://www.sciencedirect.com/science/article/pii/S2589004224026294Cell biologyData analysisMachine learning
spellingShingle Daniel Chen
Tempest Plott
Michael Wiest
Will Van Trump
Ben Komalo
Dat Nguyen
Charlie Marsh
Jarred Heinrich
Colin J. Fuller
Lauren Nicolaisen
Elisa Cambronero
An Nguyen
Christian Elabd
Francesco Rubbo
Rachel DeVay Jacobson
A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
iScience
Cell biology
Data analysis
Machine learning
title A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
title_full A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
title_fullStr A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
title_full_unstemmed A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
title_short A combined AI and cell biology approach surfaces targets and mechanistically distinct Inflammasome inhibitors
title_sort combined ai and cell biology approach surfaces targets and mechanistically distinct inflammasome inhibitors
topic Cell biology
Data analysis
Machine learning
url http://www.sciencedirect.com/science/article/pii/S2589004224026294
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