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Liver gene therapy with intein‐mediated F8 trans‐splicing corrects mouse haemophilia A by Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, Stefano Auricchio, Antonella Iuliano, Edoardo Nusco, Simone Merlin, Cristina Olgasi, Giorgia Manni, Marco Gargaro, Francesca Fallarino, Antonia Follenzi, Alberto Auricchio
Published 2022-05-01Get full text
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