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Case Report: Eltrombopag in mosaic and gene therapy-treated patients with Fanconi anemia by Josune Zubicaray, June Iriondo, Elena Sebastián, Alejandro Sanz, Paula Rio, Jean Soulier, Sonsoles San Román, José J. Uriz, Susana Navarro, Eileen Nicoletti, Juan A. Bueren, Jonathan D. Schwartz, Julián Sevilla
Published 2025-08-01Get full text
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